Login to Your Account

Work's nice if you can get it?
Researchers reported Friday that in primates, the experimental antibody cocktail Zmapp could reverse Ebola disease in monkeys when it was administered up to five days after infection, at a point where the animals were severely ill. more »

Our Habitat for All Things Science
Promising compounds 'profoundly alter' disease course in SMA

Scientists from Roche Pharma Research and Early Development (pRED) and PTC Therapeutics Inc., with colleagues in academia, reported on small-molecule drugs that improved the symptoms of spinal muscular atrophy (SMA) by altering the splicing of the protein SMN2.

In mouse models of SMA, the compounds "profoundly altered the course of the disease," PTC Therapeutics CEO and co-author Stuart Peltz told BioWorld Today.



Partners in Focus