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Thanks for the memories

"Recalling a memory is not like playing a tape recorder," Susumu Tonegawa told reporters. "It is a creative process." Normally, that creativity comes from the organism – man or mouse – doing the remembering. more »

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Promising compounds 'profoundly alter' disease course in SMA

Scientists from Roche Pharma Research and Early Development (pRED) and PTC Therapeutics Inc., with colleagues in academia, reported on small-molecule drugs that improved the symptoms of spinal muscular atrophy (SMA) by altering the splicing of the protein SMN2.

In mouse models of SMA, the compounds "profoundly altered the course of the disease," PTC Therapeutics CEO and co-author Stuart Peltz told BioWorld Today.



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