FDA approves IND for first-in-human study of CRISPR therapeutic CRD-TMH-001
Aug. 11, 2022
Cure Rare Disease (CRD) announced that the FDA has approved the first-in-human IND for CRD-TMH-001, its first therapeutic candidate using CRISPR-transactivator technology to treat a rare mutation causing Duchenne muscular dystrophy.