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BioWorld - Wednesday, May 14, 2025
Breaking News: 100 days of uncertaintySee today's BioWorld Science
Home » OT-004 delivers RPGRIP1 gene and stabilizes visual loss in murine model
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Ocular

OT-004 delivers RPGRIP1 gene and stabilizes visual loss in murine model

May 30, 2023
Mutations in the RPGRIP1 gene are associated with rare retinal dystrophies and most commonly with Leber congenital amaurosis (LCA) type 6, which is characterized by vision loss, among other symptoms.
BioWorld Science Conferences Genetic/congenital Ocular Gene therapy

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