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BioWorld - Tuesday, May 13, 2025
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Home » Pharming’s PI3K-delta inhibitor, Joenja, wins first FDA nod in APDS
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Pharming’s PI3K-delta inhibitor, Joenja, wins first FDA nod in APDS

March 24, 2023
By Jennifer Boggs and Karen Carey
Pharming Group NV’s stock skyrocketed March 24 on news that the U.S. FDA approved Joenja (leniolisib) to treat activated phosphoinositide 3-kinase delta syndrome (APDS) for those ages 12 and older. The nod, which came a few days ahead of the March 29 PDUFA date, sent shares (NASDAQ:PHAR) up 33%, or $3.69, to end the day at $14.96.
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