Login to Your Account

Clinic Roundup

Tuesday, December 20, 2011
• Isis Pharmaceuticals Inc., of Carlsbad, Calif., initiated a Phase I study of ISIS-SMNRx in patients with spinal muscular atrophy (SMA). The single-dose, dose-escalation study is designed to assess the safety, tolerability and pharmacokinetic profile of the drug in children with SMA between the ages of 2 and 14 who are medically stable. ISIS-SMNRx will be administered intrathecally as a single injection directly into the spinal fluid.

To continue reading subscribe now to BioWorld Today

Learn More about BioWorld Today

Already a subscriber? Sign In or Buy now to activate your subscription