Company*
(Country;
Symbol)

Product

Description

Indication

Status
(Date)


AUTOIMMUNE

Alba
Therapeutics
Corp.*

AT-1001

Oral zonulin receptor antagonist

Celiac disease

Began Phase I trial that will evaluate safety, tolerability and pharmacokinetics in 24 volunteers (9/27)

Arakis Ltd.
(UK; unit of
Sosei Co. Ltd.)

AD 452

Small-molecule, disease- modifying anti-rheumatic agent

Rheumatoid arthritis

Began Phase IIb trial with methotrexate to evaluate efficacy and safety in 292 patients (9/5)

Chiron Corp.
(CHIR) and
Berlex Inc.

Betaseron (FDA-approved)

Interferon beta-1b

Multiple sclerosis

Preliminary 16-year follow-up data showed advantages for the drug group vs. placebo (9/27); BENEFIT trial showed drug reduced the risk of developing clinically definite MS by 50% vs. placebo (9/30)

Genzyme
Corp.
(GENZ)

Campath (FDA- pproved)

Alemtuzumab; humanized monoclonal antibody that binds to CD52 on cell surfaces

Multiple sclerosis

One-year data from Phase II trial vs. Rebif showed advantage in the Campath arm, but dosing was stopped after three cases of severe idiopathic thrombocy- topenic purpura were seen (9/16)

Protalex Inc.
(OTC BB:PRTX)

PRTX-100

Bioregulatory compound designed to normalize the activity of immune cells

Rheumatoid arthritis

Starting Phase I trials following the FDA's lifting of a clinical hold on the product (9/13)

Synta
Pharmaceuticals
Corp.*

STA-5326

Small-molecule, selective inhibitor of the IL-12 cytokine family

Crohn's disease

Began Phase IIb SCORE trial to evaluate safety and efficacy; a companion study will evaluate biological markers (9/14)

CANCER

AnorMED Inc.
(Canada; TSE:AOM)

AMD3100

Agent designed to block receptor that triggers movement of stem cells out of bone marrow

Stem cell transplantation in cancer

Trial showed patients taking drug plus G- SF were able to collect more stem cells than those taking G-CSF alone (9/6)

Allos
Therapeutics
Inc.
(ALTH)

Efaproxyn

Efaproxiral; small molecule designed to sensitize hypoxic areas of tumors during radiation therapy

Unresectable non-small-cell lung cancer

Phase II trial in 51 patients suggest adding drug to sequential chemoradiotherapy may improve survival over S-CRT alone without increasing radiation toxicity (9/1)

Antisoma plc
(UK; LSE:ASM)

AS1411

Anti-nucleolin aptamer

Cancers

The company re-opened a Phase I trial in patients with renal and non-small-cell lung cancers (9/6)

A.P. Pharma
Inc.
(APPA)

APF530

The anti-emetic granisetron in a polymer-based drug delivery system

Chemotherapy- induced nausea and vomiting

Phase II trial in 45 patients met safety, pharmacokinetic and tolerability endpoints; evidence of efficacy was seen (9/29)

Avalon
Pharmaceuticals
Inc.
(AVRX)

AVN944

Small-molecule inhibitor of the enzyme inosine monophosphate dehydroenase

Advanced hematological malignancies

Got OK to start Phase I trial in patients (9/30)

Cell
Therapeutics
Inc.
(CTIC)

Xyotax

Paclitaxel linked to a biodegradable polyglutamate polymer

Advanced non-small-cell lung cancer

Data from PGT202 trial and from pooled data showed statistically significant survival advantage for women vs. men (9/27)

ChemGenex
Pharmaceuticals
Ltd.
(Australia;
CXSP)

Quinamed

Naphthalimide analogue; topoisomerase II inhibitor

Cancers

Phase II trial in prostate cancer was expanded to include patients with breast and ovarian cancers (9/26)

CuraGen Corp.
(CRGN) and
TopoTarget
A/S*
(Denmark)

PXD101

Small-molecule histone deacetylase inhibitor

Advanced colorectal cancer

Began Phase Ib trial to establish the maximum dose with 5-FU in up to 15 patients; then up to 20 patients with advanced colorectal cancer will be tested(9/27)

CuraGen Corp.
(CRGN) and
TopoTarget
A/S*
(Denmark)

PXD101

Small-molecule histone deacetylase inhibitor

Advanced solid tumors

Began Phase Ib trial to establish the maximum dose with carbo-platin and/or paclitaxel in up to 30 patients; afterward, 15 ovarian cancer patients will be added (9/13)

Cytheris SA*
(France)

--

Recombinant interleukin-
7; a growth factor

Myeloid
malignancies

Began Phase I trial in patients who underwent a T-cell-depleted allogenic hematopoietic cell transplant (9/19)

Cytokinetics
Inc.
(CYTK)

Ispinesib
(SB-715992)

Small-molecule inhibitor of kinesin spindle protein

Advanced breast cancer

Phase II trial will proceed after interim analysis demonstrated sufficient activity (9/27)

Cytokinetics
Inc.
(CYTK)

Ispinesib (SB-715992)

Small-molecule inhibitor of kinesin spindle protein

Non-small-cell lung cancer

Phase II trial did not demonstrate sufficient activity to proceed in platinum-refractory arm of Phase II trial (9/27)

EntreMed
Inc.
(ENMD)

Panzem

2-methoxyestradiol; naturally occurring metabolite of endogenous estrogen

Refractory prostate cancer

Phase II trial in 33 patients showed tolerability and reductions in PSA levels (9/27)

Exelixis Inc.
(EXEL)

XL844

Oral inhibitor of the protein kinases Chk 1 and 2

Chronic lymphocytic leukemia

Began Phase I trial to evaluate safety, tolerability and pharmaco-kinetics in patients (9/22)

Exelixis Inc.
(EXEL)

XL184

Agent believed to inhibit the hepatocyte growth factor receptor and VEGF-2

Advanced solid tumors

Began Phase I trial to evaluate safety, tolerability and pharmaco-
kinetics in patients (9/22)

Genentech Inc.
(NYSE:DNA)

Avastin (FDA-approved)

Bevacizumab; antibody designed to inhibit vascular endothelial growth factor

Refractory ovarian cancer

Stopped enrollment in Phase II trial due to a higher rate of gastrointestinal perforations reported than in previous trials (9/23)

Genentech Inc.
(NYSE:DNA)

Herceptin
(FDA-approved)

Trastuzumab; monoclonal antibody against HER2/neu protein

Early stage breast cancer

Interim data from Phase III trial with chemotherapy showed a significant reduction in disease recurrence in HER- positive early stage disease (9/13)

Genta Inc.
(GNTA)

Genasense

Oblimersen sodium; inhibits function of bcl-2 protein

Relapsed/ refractory chronic lymphocytic leukemia

Extended follow-up results from Phase III trial with chemotherapy showed significantly longer remission duration and significantly lower risk of relapse (9/19)

GlycoGenesys
Inc.
(GLGS)

GCS-100

Complex carbohydrate agent

Solid tumors

Phase I trial established the maximum dose, demonstrated safety and tolerability and provided evidence of disease stability (9/8)

Greenwich
Therapeutics
Inc.*

SSG

Sodium stibogluconate; targets a class of enzymes in cells

Cancers

Began Phase I trial to evaluate safety, tolerability, efficacy and dosing with interferon alpha-2b in 24 patients (9/13)

Hana
Biosciences
Inc.
(OTC BB:HNAB)

IPdR

Orally available thymidine analogue; prodrug of IUdR

Cancers

Began Phase I trial in patients to evaluate safety, dosing and preliminary efficacy in combination with radiation therapy (9/7)

IDM Pharma
Inc.
(IDMI)

Uvidem

Vaccine consisting of mature dendritic cells loaded with lysates of tumor cell lines

Melanoma

Began second stage of Phase II trial in 25 patients after first stage in 12 patients met response criteria (9/27)

ImmunoGen
Inc.
(IMGN)

huN901-DM1

Antibody designed to deliver DM1 to CD56- expressing cancer cells

Multiple myeloma

Began Phase I trial to evaluate safety, dosing and anticancer activity (9/7)

Introgen
Therapeutics
Inc.
(INGN)

INGN 225

Product using Advexin to stimulate dendritic cells, which are then used as a therapeutic vaccine

Advanced small-cell lung cancer

Interim data from ongoing Phase II trial showed vaccine was well tolerated and appeared to sensitize tumors to additional chemotherapy (9/12)

NeoPharm
Inc.
(NEOL)

LEP-ETU

Liposomal formulation of paclitaxel

Cancers

The product met study criteria in demonstrating bioequivalence to paclitaxel (Taxol) (9/29)

OncoGenex
Technologies
Inc.*
(Canada)
and Isis
Pharmaceuticals
Inc.
(ISIS)

OGX-011

Second-generation anti- sense drug designed to inhibit the production of clusterin, a cell-survival protein

Prostate cancer

Phase I trial demonstrated tolerability and reduced clusterin expression (9/7)

Oncolytics
Biotech Inc.
(Canada; ONCY)

Reolysin

Formulation of the human reovirus

Advanced solid tumors

Began Phase I trial to evaluate dosing, safety and actvity in up to 36 patients (9/28)

OxiGene Inc.
(OXGN)

CA4P

Combretastatin A4 prodrug; a vascular targeting agent

Advanced ovarian cancer

Began Phase II trial to evaluate the drug with carboplatin and paclitaxel in platinum- resistant disease (9/21)

rOxxon
Therapeutics
Inc.*

--

PrimeBoost immuno-therapeutic platform

Metastatic melanoma

Data from ongoing Phase II trial demonstrated safety, tolerability and immune responses (9/7)

Peplin Ltd.
(Australia;
ASX:PEP)

PEP005 Topical

Agent designed to kill cancer cells and stimulate an immune response

Actinic keratosis

Began Phase IIa trial in 13 to 34 patients to determine the maximum tolerated dose (9/1)

Pharmacyclics
Inc.
(PCYC)

Xcytrin

Motexafin gadolinium; small molecule from the texaphyrin class designed to induce apoptosis

Brain metastases from solid tumors

Began Phase II trial to evaluate the drug with whole-brain radiation therapy and stereotactic radiosurgery in 45 patients(9/13)

Pharmacyclics
Inc.
(PCYC)

Xcytrin

Motexafin gadolinium; small molecule from the texaphyrin class designed to induce apoptosis

Advanced non- small-cell lung cancer

Began Phase II trial to evaluate safety and efficacy as a second- line treatment in 108 patients (9/8)

Point
Therapeutics
Inc.
(POTP)

Talabostat

Small molecule designed to stimulate proliferation of hematopoietic progenitor cells

Advanced chronic lymphocytic leukemia

Data from first 20 patients in Phase II trial with rituximab showed a 20% response rate, the rate needed to continue the trial(9/19)

Sonus
Pharmaceuticals
Inc.
(SNUS)

Tocosol
Paclitaxel

Formulation of paclitaxel
using Sonus' delivery
system

Metastatic breast cancer

Began pivotal trial under FDA SPA to evaluate response rate and other endpoints in 828 patients (9/28)

ViaCell Inc.
(VIAC)

CB001

Hematopoietic stem cells selectively amplified from umbilical cord blood

Stem cell transplants in cancer applications

Suspended enrollment in Phase I trial; 2 of 8 treated patients experienced Grade IV acute graft vs host disease (9/19); the FDA placed a hold on the trial (9/21)

Vion
Pharmaceuticals
Inc.
(VION)

Cloretazine (VNP40101M)

Sulfonylhydrazine DNA alkylating agent

Advanced small-cell lung cancer

Began Phase II trial to evaluate responses and toxicity in patients who did not respond to or relapsed after initial treatment (9/20)

Viventia
Biotech Inc.
(Canada; TSE:VBI)

Proxinium

Antibody fragment conjugated with a cancer-killing payload

Refractory head and neck cancer

Starting a Phase II trial in the U.S. in patients with recurrent disease (9/19)

CARDIOVASCULAR

Amarillo
Biosciences
Inc.
(OTC BB:AMAR)

--

Low-dose oral interferon alpha

Bone marrow proliferative disorders

Began trial to test product in 20 patients with either polycythemia vera or primary thrombocythemia (9/22)

Amgen
Inc.
(AMGN)

Aranesp (FDA-approved)

Darbepoetin alfa, a recombinant erythropoietic protein

Heart failure

Began Phase III trial to evaluate anemia treatment on morbidity and mortality in patients with heart failure (9/2)

Archemix Corp.*
and Nuvelo Inc.
(NUVO)

ARC183

Anti-thrombin aptamer

Anticoagulant

They ended development of the product after determining in a Phase I trial that it had a suboptimal dosing profile (9/21)

Cardiome
Pharma Corp.
(Canada; CRME)

RSD1235

Oral formulation of drug designed to selectively block ion channels in the heart

Atrial arrhythmia

Phase III ACT 3 trial in 276 patients achieved statistical significance vs. placebo in conversion to normal heart rhythm (9/29)

Cytokinetics
Inc.
(CYTK)

CK-1827452

Small-molecule activator of cardiac myosin

Heart failure

Began Phase I trial to evaluate safety, tolerability and pharmaco-kinetics in healthy volunteers (9/6)

Encysive
Pharmaceuticals
Inc.
(ENCY)

Thelin

Sitaxsentan; small molecule designed to block endothelin

Pulmonary arterial hypertension

Extension study from Phase III STRIDE 2 trial showed advantages vs. bosentan in some endpoints (9/14)

Isis
Pharmaceuticals
Inc.
(ISIS)

ISIS 301012

Capsule formulation of second-generation anti- sense inhibitor of ApoB-100

Cholesterol management

Began a Phase II trial that will evaluate dosing, safety and efficacy in patients with high cholesterol (9/20)

Microbia Inc.*

MD-0727

Cholesterol absorption inhibitor

High cholesterol

Began Phase I trial to evaluate safety, tolerability and pharmaco-kinetics in healthy volunteers (9/15)

NitroMed Inc.
(NTMD)

BiDil (FDA-approved)

Nitric oxide-enhancing oral agent; combination of isosorbide dinitrate and hydralazine

Heart failure in African-Americans

Data from A-HeFT trial suggested drug can inhibit left ventricular remodeling in patients with severe heart failure (9/21)

Nuvelo Inc.
(NUVO)

Alfimeprase

Modified fibrolase delivered via catheter; thrombolytic agent

Central venous catheter occlusion

Began Phase III SONOMA-2 trial to assess of catheter function vs. placebo in 300 patients (9/7)

Viron
Therapeutics
Inc.*
(Canada)

VT-111

Virally derived anti- inflammatory protein

Acute coronary syndromes

Began Phase II trial to evaluate safety and efficacy trends in 72 patients (9/26)

CENTRAL NERVOUS SYSTEM

Adolor Corp.
(ADLR)

--

Lidocaine patch

Post-surgical incisional pain

Began Phase II trial named Study 29CL227(9/15)

Aeolus
Pharmaceuticals
Inc.
(OTC BB:AOLS)

AEOL 10150

Small-molecule catalytic antioxidant

Amyotrophic lateral sclerosis

Phase I trial in 25 patients showed tolerability and no drug-related cardiovascular abnormalities (9/6)

Axonyx
Inc.
(AXYX)

Phenserine

Inhibitor of acetylcholin- esterase and beta-amyloid precursor protein

Alzheimer's disease

Data from two curtailed Phase III trials did not demonstrate a statistically significant benefit vs. placebo (9/20)

Ceregene Inc.*

CERE-120

Gene therapy product that delivers the neurturin gene via an adeno-associated virus Type II vector

Parkinson's disease

Began a Phase I trial that will evaluate safety and efficacy in PD patients (9/21)

Cypress Bioscience Inc.
(CYPB) and
Forest
Laboratories Inc.

Milnacipran

Norepinephrine serotonin reuptake inhibitors

Fibromyalgia

Pivotal Phase III trial in 888 patients failed to achieve statistical significance; the plan is to continue development (9/28)

CytRx Corp.
(CYTR)

Arimoclomol

Small molecule designed to provide cellular protection by activating molecular chaperone proteins

Amyotrophic lateral sclerosis

Began Phase II trial to evaluate safety, tolerability and efficacy in 80 patients (9/22)

DOV
Pharmaceutical
Inc.
(DOVP)

DOV 216,303

Triple reuptake inhibitor

Depression

Both drug and citalopram groups showed improvements from baseline in Phase II trial in 67 patients (9/27)

DOV
Pharmaceutical
Inc.
(DOVP)

Bicifadine

Serotonin and norepinephrine reuptake inhibitor

Post-operative pain

Phase III trial in 350 patients following bunionectomy surgery showed statistically significant analgesic effects at 400 mg vs. placebo (9/12)

Myriad
Genetics Inc.
(MYGN)

Flurizan

Selective amyloid beta 42 lowering agent

Alzheimer's disease

Follow-on data from Phase II trial showed patients appeared to have no further decline in cognitive function from months 12 to 15 (9/22)

Neurogen
Corp.
(NRGN)

NG2-73

Selective modulator of gamma aminobutyric (GABA) receptors

Insomnia

Phase I trial in healthy volunteers showed the drug was safe and well tolerated and produced sleepiness (9/22)

Neurologix
Inc.
(OTC BB:NRGX)

--

Adeno-associated virus delivering gene encoding glutamic acid decarboxylase

Parkinson's disease

Phase I trial in 12 patients showed a statistically significant (27%) improvement in motor function on the side of their body correlating to the treated part of the brain (9/26)

New River
Pharmaceuticals
Inc.
(NRPH)

NRP290

Hydrocodone derivative

Pain

Pharmacokinetic trial in healthy volunteers demonstrated bio-availability (9/12)

Pain
Therapeutics
Inc.
(PTIE)

Remoxy

Abuse-resistant form of long-acting oxycodone

Chronic pain

Phase III trial in 209 osteoarthritic patients showed a statistically significant improvement in pain relief vs. placebo (9/9)

Pharmos
Corp.
(PARS)

Cannabinor

CB2-selective synthetic cannabinoid agent

Pain

Began Phase I trial to evaluate safety, tolerability and pharmaco-kinetics in up to 48 healthy volunteers (9/6)

Proneuron
Biotechnologies
Inc.*

ProCord

Autologous incubated macrophage therapy

Acute spinal cord injury

Phase I trial in eight patients showed therapy was well tolerated; preliminary signs of efficacy were seen (9/12)

Sepracor
Inc.
(SEPR)

Lunesta (FDA-approved)

Eszopiclone tablets; a non-enzodiazepine agent

Insomnia

Phase IIIb/IV trial in 410 perimenopausal and menopausal women demonstrated statistical significance in various endpoints (9/30)

Sepracor
Inc.
(SEPR)

Lunesta (FDA-approved)

Eszopiclone tablets; a non-enzodiazepine agent

Insomnia

Six-month Phase IIIb/IV trial in 828 patients demonstrated statistical significance in various end-points (9/28)

Somaxon
Pharmaceuticals
Inc.*

Silenor

Low dose of the approved depression drug doxepin

Insomnia

Began a second Phase III trial, which will evaluate safety and efficacy in elderly patients (9/20)

DIABETES

Alkermes Inc.
(ALKS) and
Eli Lilly and Co.

--

Inhaled insulin powder system based on Alkermes' AIR delivery technology

Type I diabetes

Phase II trial showed blood sugar levels similar to patients treated with injected insulin; 80% of patients preferred inhaled product vs. injected insulin (9/12)

CardioVascular
BioTherapeutics
Inc.
(OTC BB:CVBT)

Cardio Vascu-Grow

Stimulator of angiogenesis

Diabetic foot ulcers and wounds

Starting a Phase I trial to test the safety and tolerability of the agent (9/13)

ConjuChem
Inc.
(Canada;
TSE:CJC)

DAC:GLP-1

Insulinotropic hormone GLP created with firm's DAC technology

Diabetes

Further development activities were put on hold pending completion of Phase I trials of a potentially better product (9/30)

Cytomedix
Inc.
(AMEX:GTF)

AutoloGel

Platelet releasate therapy system

Diabetic foot ulcers

Preliminary analysis of trial showed potentially similar efficacy as the standard therapy (9/12)

INFECTION

Arrow
Therapeutics
Ltd.*
(UK)

A-60444

Small-molecule inhibitor of protein involved in viral replication

Respiratory syncytial virus

Got OK to expand its Phase IIa trial into the U.S. in adult patients infected with RSV after bone marrow transplantation (9/12)

AVI
BioPharma
Inc.
(AVII)

AVI-4065

Neugene antisense compound

Hepatitis C

Began exploratory trial to assess safety, tolerability, pharmacokinetics and viral response in 40 healthy volunteers followed by 40 patients (9/28)

BioAlliance
Pharma SA*
(France)

Miconazole Lauriad

Oral, bioadhesive buccal tablet containing the antifungal miconazole

Oropharyngeal candidiasis

Starting a pivotal Phase III trial in the U.S. in HIV-positive patients (9/6)

Coley
Pharmaceutical
Group Inc.
(COLY)

Actilon (CPG 10101)

Agent designed to target and stimulate Toll-like receptor 9

Hepatitis C

Began Phase Ib trial to assess safety, tolerability and virus levels in 60 patients separated into various regimens (9/27)

CytRx Corp.
(CYTR)

DP6-001

Vaccine formulation based on five strains of HIV

HIV

Phase I trial showed vaccine was well tolerated, stimulated T cells and produced antibody responses against multiple HIV strains (9/7)

GenVec Inc.
(GNVC)

--

Adenovector-based booster HIV vaccine developed with the Vaccine Research Center

HIV

Data from eight healthy volunteers in Phase I trial showed tolerability and a cellular and antibody immune response (9/7)

IDM Pharma
Inc.
(IDMI)

EP HIV-1090

HIV DNA vaccine

HIV

Phase I trial in 40 patients established safety and the utility of DNA vaccines for the delivery of multiple CTL epitopes (9/7)

Inhibitex
Inc.
(INHX)

Veronate

Antibody-based immune globulin

S. aureus infections in low-birth-weight infants

Monitors recommended Phase III trial continue after reviewing data on 1,500 patients (9/6)

MedImmune
Inc.
(MEDI)

Numax

Motavizumab; third- generation variant of the anti-RSV antibody Synagis

Respiratory syncytial virus

Phase I trial in 30 infants showed drug appeared to be safe and reduced RSV in the upper respiratory tract (9/1)

Nabi Bio-
pharmaceuticals
(NABI)

StaphVAX vaccine

Staphylococcus aureus polysaccharide conjugate infections

To prevent S. aureus

Immunogenicity trial showed 94% of patients undergoing orthopedic surgery with a prosthetic device implant achieved desired antibody levels (9/29)

Nabi Bio-
pharmaceuticals
(NABI)

StaphVAX

Staphylococcus aureus polysaccharide conjugate vaccine

To prevent S. aureus infections

Began trial to evaluate vaccine in a subset of 460 end-stage renal disease patients from ongoing Phase III trial (9/20)

Oscient
Pharmaceuticals
Corp.
(OSCI)

Factive (FDA-approved)

Gemifloxacin mesylate; a fluoroquinolone antibiotic

Community- acquired pneumonia

Final data from pivotal Phase III trial showed non-inferiority of five-day treatment vs. the approved seven-day treatment (9/19)

Progenics
Pharmaceuticals
Inc.
(PGNX)

PRO 140

Humanized monoclonal antibody against CCR5; HIV entry inhibitor

HIV

Dose-dependent binding of PRO 140 to CCR5-expressing cells was seen in a Phase I trial (9/9)

Tanox Inc.
(TNOX)

TNX-355

Humanized anti-CD4 monoclonal antibody; designed to inhibit viral entry

HIV

Monitors recommended continuation of Phase II trial after planned 20-week interim safety analysis (9/13)

XTL Bio-
pharmaceuticals
Ltd.
(Israel; XTLB)

XTL-6865

Combination of two fully human monoclonal antibodies (Ab68 and Ab65) against the HCV E2 envelope protein

Hepatitis C

Began a Phase Ia trial in the U.S. and Israel (9/29)

MISCELLANEOUS

Adolor Corp.
(ADLR) and
GlaxoSmithKline
plc
(UK)

Entereg

Alvimopan capsules; mu opioid antagonist

Opioid-induced constipation

Began Phase III trial that will assess efficacy vs. placebo in about 1,700 patients (9/12)

Altus
Pharmaceuticals
Inc.*

ALTU-238

Long-acting, crystalline formulation of recombinant human growth hormone

Growth hormone deficiency

Presented positve data from Phase I trial in healthy adults, and began Phase II trial (9/28)

Biovitrum AB*
(Sweden)

BVT.28949

Agent in eye-drop form designed to lower intraocular pressure by increasing the outflow of aqueous humor

Glaucoma

Began Phase I trial to test safety in 60 healthy volunteers (9/13)

Discovery
Laboratories
Inc.
(DSCO)

Aerosurf

Aerosolized surfactant replacement therapy

Respiratory distress syndrome in premature babies

Pilot Phase II trial in 17 infants demonstrated feasibility of delivery, and that treatment was generally safe and well tolerated (9/8)

Discovery
Laboratories
Inc.
(DSCO)

Surfaxin

Engineered version of natural human lung surfactant

Respiratory distress syndrome in premature babies

Analysis vs. animal-derived surfactants showed advantages in survival, days in intensive care and hospital costs (9/1)

Exelixis Inc.
(EXEL)

XL784

Inhibitor of the ADAM-10 matrix metalloprotease enzyme

Renal failure

Began repeat-dose Phase I trial in healthy volunteers to prepare for a Phase II program (9/22)

Genzyme
Corp.
(GENZ)

Myozyme

Recombinant human acid alpha-lucosidase enzyme

Late-onset Pompe disease

Began trial to evaluate safety and efficacy in at least 72 patients (9/15)

Genzyme
Corp.
(GENZ)

Renagel (FDA-approved)

Sevelamer hydrochloride; phosphate binder

Renal disease

RIND trial in 129 patients new to dialysis showed a statistically significant improvement in coronary artery calcification vs. calcium-based phosphate binders (9/29)

GTx Inc.
(GTXI)

Ostarine

Selective androgen receptor modulator

Muscle wasting associated with burns

Reported positive results from Phase I trial (9/7)

Indevus
Pharmaceuticals
Inc.
(IDEV)

Sanctura XR

Once-daily version of FDA-approved trospium chloride agent

Overactive bladder

Began Phase III program consisting of two 12-week studies that will evaluate efficacy in 1,200 patients (9/8)

ISTA
Pharmaceuticals
Inc.
(ISTA)

Vitrase (FDA-approved)

Ovine hyaluronidase formulation

Vitreous hemorrhage

Pooled data from Phase III studies demonstrated a statistically significant reduction in vitreous hemorrhage density (9/7)

Nastech
Pharmaceutical
Co. Inc.
(NSTK)

PTH1-34

Intranasal formulation of a fragment of naturally occurring human parathyroid hormone

Osteoporosis

Phase I trial in 12 healthy subjects achieved its pharmacokinetic and safety goals (9/29)

NPS
Pharmaceuticals
Inc.
(NPSP)

Preos

Recombinant human parathyroid hormone

Osteoporosis

New analysis from several trials showed improved bone strength and architecture and reduced risk of vertebral fracture (9/27)

Nymox
Pharmaceutical
Corp.
(NYMX)

NX-1207

Investigational agent for BPH

Benign prostatic hyperplasia

Interim review of safety data from Phase II trial revealed no serious side effects or safety issues (9/14)

QLT Inc.
(Canada; QLTI)

Visudyne (FDA-approved)

Verteporfin for injection; aphotodynamic therapy

Wet age-related macular degeneration

Visudyne in occult trial did not achieve the primary endpoint at two years in patients with pre-dominantly occult CNV (9/20)

Tercica Inc.
(TRCA)

Increlex (FDA-approved)

Mecasermin injection; recombinant human insulin-like growth factor-1

Short stature caused by IGF deficiency

Long-term data showed the drug appeared to improve statural growth and generally was well tolrated (9/23)


Notes:

* Privately held.

BLA = Biologics license application; FDA = Food and Drug Administration; IND = Investigational new drug application; NDA = New drug application; SPA = Special protocol assessment.

Unless otherwise noted, the stock symbols listed for public companies are on the Nasdaq market.

AMEX = American Stock Exchange; ASX = Australian Stock Exchange; LSE = London Stock Exchange; NYSE = New York Stock Exchange; OTC BB = Over-the-Counter Bulletin Board; TSE = Toronto Stock Exchange.