Company*
(Country;
Symbol)

Product

Description

Indication

Status
(Date)


AUTOIMMUNE

4SC AG*
(Germany)

SC12267

Small molecule designed to inhibit pyrimidine synthesis

Autoimmune diseases

Phase I trial demonstrated safety, tolerability and a good pharmacokinetic profile (3/24)

CANCER

Adherex
Technologies
Inc.
(AMEX:ADH)

Exherin (ADH-1)

Cadherin antagonist; small-peptide, tumor/ vascular-targeting agent

Various cancers

Began Phase II trial in Canada to test the drug in eight tumor types in 60 patients whose tumors express N-cadherin (3/24)

Alfacell Corp.
(ACEL)

Onconase

Ranpirnase; cytotoxic ribonuclease

Malignant mesothelioma

The product was granted orphan designation in Australia in that indication (3/28)

Bioenvision
Inc.
(BIVN)

Clofarabine

Second-generation purine nucleoside analogue

Pediatric and adult acute leukemia

Presented data from ongoing trials that confirm positive data from previous studies (3/21)

GammaCan
International
Inc.
(Israel;
OTC BB:GCAN)

GCAN 101

Therapy based on intravenous immuno- globulin

Cancers

Began Phase II trial in up to 30 patients with metastatic melanoma, metastatic prostate or colon cancers (3/14)

Genzyme
Corp.
(GENZ)

Thyrogen
(FDA-approved)

Thyrotropin alfa for injection; a recombinanthuman thyroid- stimulating hormone

Ablation of remnant thyroid tissue

The European Commission approved the product for use with radio-iodine (3/3)

Maxim
Pharmaceuticals
Inc.
(MAXM)

Ceplene

Histamine dihydrochloride in combination with interleukin-2

Acute myeloid leukemia

The product was granted orphan designation in Europe in that indication (3/9)

OSI
Pharmaceuticals
Inc.
(OSIP) and
Genentech
Inc.
(NYSE:DNA)

Tarceva (FDA-approved)

Erlotinib HCl; small- molecule HER1/EGFR inhibitor

Advanced non- small-cell lung cancer

The product was approved in Switzerland for treating locally advanced or metastatic disease; F. Hoffmann-La Roche Ltd. has marketing rights in Europe (3/22)

Oxford
BioMedica
plc
(UK; LSE:OXB)

TroVax

Vaccine that delivers an antigen (5T4) using a poxvirus vector

Metastatic colorectal cancer

The primary endpoints of safety and immunological responses were achieved in Phase II trials with chemotherapy in 25 patients; clinical benefit also was seen; in another trial all eight evaluable patients mounted immune responses (3/2)

Praecis
Pharmaceuticals
Inc.
(PRCS)

Plenaxis (FDA-approved)

Abarelix for injectable suspension; gonadotropin- releasing hormone antagonist

Prostate cancer

German authorities had questions about the MAA that could impact future labeling (3/24)

Psiron Ltd.
(Australia; ASX:PSX)

CVA21

Coxsackie A21 (common cold) virus

Advanced melanoma

Began initial human testing of the product in two patients; initial data showed it was well tolerated (3/15)

CARDIOVASCULAR

GTC
Biotherapeutics
Inc.
(GTCB)

ATryn

Recombinant human antithrombin

Hereditary antithrombin deficiency

The EMEA has questions on the MAA, which was filed in February 2004, delaying the expected time to launch (3/16)

NicOx SA
(France; Eurolist:
NICOX)

NCX 4016

Nitric oxide-donating derivative of aspirin

Cardiovascular complications

Phase IIa trial in 40 patients showed drug was more effective than aspirin and placebo at prventing platelet activation induced by acute hyperglycemia in diabetic patients (3/1)

United
Therapeutics
Corp.
(UTHR)

Remodulin (FDA-approved)

Treprostinil sodium injection

Pulmonary hypertension

French officials issued an approval letter for treating NYHA Class III primary PH, and said the mutual recognition process in the EU would begin in May (3/8)

CENTRAL NERVOUS SYSTEM

Axonyx
Inc.
(AXYX)

Phenserine

Inhibitor of acetylcholin- esterase and beta-amyloid precursor protein

Alzheimer's disease

Company released additional details from Phase III trial in 375 patients in Europe that failed to demonstrate statistical significance, and halted additional recruitment in Phase III trials; a Phase IIb trial continues (3/11)

Cara
Therapeutics
Inc.*

CR665

Selective peripheral kappa opioid receptor agonist

Pain

Began Phase I trial in the UK to test safety, tolerability and pharmacokinetics in healthy volunteers (3/24)

LAB International
Inc.
(Canada;
TSE:LAB)

Fentanyl Taifun

Fentanyl formulation delivered via the company's dry powder inhaler platform

Pain in cancer patients

Began Phase II trial in 112 patients to evaluate safety and efficacy (3/29)

Prana
Biotechnology
Ltd.
(Australia;
ASX:PBT)

PBT2

Small molecule that binds metal ions

Alzheimer's disease

Began Phase I trial in the Netherlands to examine safety and pharmacokinetics in volunteers (3/14)

DIABETES

Speedel Group*
(Switzerland)

SPP301

Once-a-day oral endothelin A receptor antagonist

Diabetic nephropathy

All doses in a Phase IIa trial in 286 patients demonstrated statistic- ally significant decreases in albumin excretion rates (3/2)

INFECTION

AEterna
Zentaris Inc.
(Canada; AEZS)

Impavido

Oral miltefosine, an alkylphospholipid agent

Cutaneous form of leishmaniasis

The product was approved in Colombia; the approval also applies to the visceral form of leishmaniasis (3/23)

Access
Pharmaceuticals
Inc.
(AMEX:AKC)

Aphthasol
(FDA-approved)

Product containing amlexanox

Canker sores

The product was approved in 10 European Union countries follow- ing completion of the Mutual Recognition Procedure (3/3)

Chiron Corp.
(CHIR)

Fluvirin (FDA-approved)

Influenza vaccine

Influenza

UK officials lifted the license suspension for Chiron's Liverpool, UK, manufacturing facility (3/2)

Enanta
Pharmaceuticals
Inc.*

EP-013420 (S-013420)

A bridged bicyclic ketolide

Infections

Partner Shionogi & Co. Ltd. began Phase I trials in Japan (3/14)

Immtech
International
Inc.
(AMEX:IMM)

DB289

Oral, dicationic antiviral agent

African sleeping sickness

All 26 patients from Phase IIb trial in the Congo remained clear of the parasite three months after concluding treatment (3/9)

Medivir AB
(Sweden; SSE:MVIR)

MIV-310

Alovudine; antiviral agent

HIV

Partner Boehringer Ingelheim stopped development after the drug did not show target efficacy in a Phase II trial (3/15)

Neutec Pharma
plc
(UK; LSE:NTP)

Mycograb

Agent based on naturally occurring antibody against hsp90

Invasive candidiasis

Began marketing application process in Europe for use in combination with amphotericin-B (3/14)

Sinovac Biotech
Inc.
(China;
AMEX:SVA)

Split influenza vaccine

Influenza

The product was approved in China (3/15)

The Immune
Response Corp.
(IMNR)

Remune

Immune-based therapy comprised of a whole-killed virus and an adjuvant

HIV

Phase II trial in Spain showed long-term treatment delayed virologic failure during antiretroviral treatment interruption; Phase II trial in Italy showed stabilization of CD4+ cell counts and positive trends in response markers (3/9)

MISCELLANEOUS

Alizyme plc
(UK; LSE:AZM)

Colal-Pred

A prednisolone derivative with Alizyme's colonic drug delivery technology

Acute ulcerative colitis

Got OK for Phase III trial in Europe that will compare the drug to conventional oral prednisolone in up to 670 patients (3/15)

BioXell SpA*
(Italy)

BXL628

Inhibitor of growth factor phosphorylation and bcl-2

Benign prostatic hyperplasia

Additional data from Phase IIa trial showed 29% of patients experienced a reduction of prostate volume vs. 0% for placebo (3/19)

Cambridge
Antibody
Technology
Group plc
(UK; CATG)

Trabio (CAT-152)

Lerdelimumab; fully human monoclonal antibody that neutralizes transforming growth factor beta-2

Glaucoma

A second pivotal Phase III trial failed to meet the primary end- point of improving the outcome of surgery for glaucoma; further development was stopped (3/22)

Cellegy
Pharmaceuticals
Inc.
(CLGY)

Rectogesic (Cellegesic)

Nitroglycerin ointment

Hemorrhoids

Trial in 47 patients in Australia showed mean anal sphincter pressure was significantly decreased; improvements were seen in pain, bleeding and other endpoints (3/28)

InKine
Pharmaceutical
Co. Inc.
(INKP)

Visicol (FDA-approved)

Sodium phosphate tablets

For use as a colonic purgative

Partner Zeria Pharmaceutical Co. Ltd. filed for approval in Japan for use as a colonic purgative, bowel cleansing agent or laxative (3/29)

Life Medical
Sciences Inc.
(OTC BB:CHAI)

Repel-CV

Bioresorbable, polymer- based adhesion barrier film

Prevention of post- operative adhesions

Began a trial to test the product at cardiac centers in Europe (3/21)

Miravant
Medical
Technologies
Inc.
(OTC BB:MRVT)

Photrex (SnET2)

Photodynamic therapy that uses a light-activated drug to destroy abnormal blood vessels

Wet age-related macular degeneration

Said it will begin a confirmatory trial in Europe in 600 patients, as called for in a September 2004 FDA approvable letter (3/10)

NicOx SA
(France; Eurolist:
NICOX)

NCX 1020

Nitric oxide-donating derivative of budesonide, a corticosteroid

Asthma

Phase IIa trial in 12 patients in the UK showed a trend in protecting against bronchoconstriction (3/15)

NPS
Pharmaceuticals
Inc.
(NPSP)

Preotact (Preos)

Recombinant human parathyroid hormone

Osteoporosis

Partner Nycomed Group submitted an MAA in Europe seeking approval for treating postmenopausal osteoporosis (3/11)

Pharming
Group NV
(the
Netherlands;
Euronext:PHARM)

rhC1INH

Recombinant human C1 inhibitor

Hereditary angioedema

Presented clinical data showing rapid time to beginning of relief and time to complete resolution, as well as favorable evaluations by patients and physicians (3/15)


Notes:

* Privately held.

MAA = Marketing authorization application; EMEA = European Medicines Agency.

Unless otherwise noted, the stock symbols listed for public companies are on the Nasdaq market.

AMEX = American Stock Exchange; ASX = Australian Stock Exchange; LSE = London Stock Exchange; NYSE = New York Stock Exchange; OTC BB = Over-the-Counter Bulletin Board; SSE = Stockholm Stock Exchange; TSE = Toronto Stock Exchange.