Company*
(Symbol)

Product

Description

Indication

Status (Date)


CANCER

AltaRex Corp. (TSE:AXO)

OvaRex

Modified murine monoclonal antibody that binds to CA125 cancer antigen

Ovarian cancer

Company reported favorable early results in a Phase II trial (10/11)

Amgen Inc.
(AMGN)

Aranesp
(FDA-
approved)

Darbepoetin alfa

Anemia in cancer patients

Clinical data showed that Aranesp reduced fatigue scores in more than half of 517 patients treated (10/23)

AnorMED
Inc.
(Canada;
TSE:AOM)

ZD0473

New-generation platinum anticancer agent

Ovarian cancer

Phase II data showed a response rate of 39% in second-line platinum- sensitive ovarian cancer patients and 7% in second-line platinum- resistant patients (10/25)

Antigenics
Inc.
(AGEN)

Oncophage

Cancer vaccine; uses heat shock proteins to activate cellular immune responses

Metastatic
melanoma

Phase II data showed responses in five of 28 evaluable patients (10/31)

Biomira
Inc.
(BIOM)

BLP25

Vaccine; synthetic MUC1 therapeutic vaccine consisting of 25-amino-acid sequence of the MUC1 cancer mucin, encapsulated in liposomes

Prostate cancer

Company initiated a Phase II trial (10/19)

Cell Genesys
Inc.
(CEGE)

GVAX

Vaccine; immuno-therapeutic comprising irradiated and genetically modified tumor cells that secrete granulocyte macrophage-colony stimulating factor

Pancreatic cancer

Company initiated a Phase II trial (10/22)

Cell Genesys
Inc.
(CEGE)

CG7870
(formerly
CV787)

Oncolytic virus engineered to target and destroy prostate cancer cells

Advanced hormone- refractory prostate cancer

Company said a Phase I/II trial demonstrated antitumor activity after a single intravenous injection (10/23)

Cell Path-
ways Inc.
(CLPA)

Aptosyn plus CPT-11

Exisulind plus camptosar, irinotecan

Colorectal cancer and other solid tumors

Phase I data showed the combination to be generally well tolerated by patients (10/31)

Cell Path-
ways Inc.
(CLPA)

CP461

Oral drug; selective apoptotic antineoplastic drug

Chronic lymphocytic leukemia

Phase IIa data showed nine of 15 patients showed a reduction from baseline in their absolute lymphocyte counts (10/9)

Cell Thera-
peutics Inc.
(CTIC)

PG-TXL

Paclitaxel/polyglutamate polymer therapeutic

Advanced cancer

Preliminary results of two trials demonstrated that PG-TXL, given alone or in combination with cisplatin, shrinks tumors in patients who have failed standard treatments (10/31)

Cell Thera-
peutics Inc.
(CTIC)

Trisenox
(FDA-
approved)

Arsenic trioxide injection

Acute promyelocytic leukemia

Data revealed that Trisenox produced a 63% overall survival rate of patients at 24 months (10/5)

ChemGenex
Therapeutics
Inc.*

Ceflatonin

A natural product compound

Acute promyelocytic leukemia

Company began patient enrollment in a pilot Phase I/II study (10/29)

Coley
Pharma-
ceutical
Group Inc.*

CpG 7909

DNA-based immune stimulant

Refractory metastatic breast cancer

Company initiated a Phase I/II trial of CpG 7909 in multidrug therapy with Genentech Inc.'s Herceptin (10/30)

Cyclacel Ltd.
(Scotland)*

CYC202

R-roscovitine; a small-molecule inhibitor of CD2

Cancer

Company completed a Phase Ia evaluation and is entering Phase Ib trials (10/15)

EntreMed
Inc.
(ENMD)

Angiostatin

Subcutaneous antiangiogenic

Advanced cancers

Phase I data showed Angiostatin is safe with no dose-limiting toxicity when combined with radiation therapy to treat advanced cancers (10/31)

Genentech
Inc.
(NYSE:
DNA)

Avastin

Bevacizumab; a humanized antibody to VEGF

Metastatic renal cell carcinoma

National Cancer Institute stopped recruitment in a Phase II trial because a monitoring board determined the trial had reached its efficacy endpoint at the second interim analysis (10/25)

Genitope
Corp.*

Idiotype immunotherapy

Therapy includes a custom-made protein derived from each patient's tumor cells

Low-grade B-cell non-Hodgkin's lymphoma

Patients are being recruited for a Phase III trial (10/2)

GenVec Inc.
(GNVC)

TNFerade

Delivers tumor necrosis factor alpha gene directly to tumors using GenVec's adenovector technology

Soft tissue sarcoma

Company began treating patients in a Phase Ib trial (10/1)

Geron Corp.
(GERN)

Telomerase

Antigen for cancer immunotherapy

Cancer

Company said Duke University Medical Center researchers initiated a Phase I trial (10/30)

Kosan
Biosciences
Inc.
(KOSN)

Epothilone D

A polyketide that inhibits
tumor cells

Advanced solid tumors

Company initiated a Phase I trial (10/29)

Lorus
Therapeutics
Inc.
(Canada;
TSE:LOR)

GTI-2040

Antisense anticancer therapeutic

Advanced or metastatic renal cell carcinoma

Company expanded the Phase II trial of GTI-2040 to be used with capecitabine (10/30)

Matrix
Pharma-
ceutical
Inc.
(MATX)

IntraDose

Cisplatin/epinephrine

Solid tumors

Phase II results showed an overall response rate of 53% in patients with inoperable primary liver cancer, a response rate of 29% in patients with head and neck cancer and a response rate of 44% in patients with metastatic melanoma (10/23)

Matrix
Pharma-
ceutical
Inc.
(MATX)

Tezacitabine

Nucleoside analogue that irreversibly inhibits ribonucleotide reductase and terminates DNA chain elongation

Acute myeloid leukemia

Company is moving forward with a Phase II study (10/11)

Maxim
Pharma-
ceuticals
Inc.
(MAXM)

Ceplene
(formerly
Maxamine)

Histamine dihydrochloride; an adjuvant to interleukin-2

Advanced metastatic melanoma

Follow-up data from a 305-patient Phase III trial, which evaluated Ceplene in combination with IL-2, were positive; the company still expects it will need to conduct another Phase III trial in order to bring Ceplene to the market (10/22)

MGI Pharma
Inc.
(MOGN)

Irofulven

Anticancer compound

Ovarian cancer

Company expanded the ongoing Phase II trial (10/11)

MGI Pharma
Inc.
(MOGN)
and Helsinn
Healthcare SA
(Switzerland)

Palonosetron

A 5-HT antagonist

Chemotherapy- induced nausea and vomiting

Companies completed enrollment in the first Phase III trial (10/3)

Millennium
Pharmaceu-
ticals Inc.
(MLNM)

LDP-341

Small-molecule proteasome inhibitor

Multiple myeloma

Company completed enrollment of a Phase II trial (10/4)

Millennium
Pharmaceu-
ticals
Inc.
(MLNM)

J591

Radiolabeled J591

Advanced prostate cancer

Phase I data showed the therapeutic demonstrated antitumor activity (10/19)

Nastech
Pharma-
ceutical Co.
Inc.
(NSTK)

Morphine gluconate

Nasal formulation

Pain in opioid- tolerant cancer patients

Company began enrollment in a Phase II trial (10/9)

NeoPharm
Inc.
(NEOL)

Liposome Encapsulated Mitoxantrone

Uses NeoLipid drug delivery system

Cancer

Company initiated a Phase I/II trial (10/4)

Novus-
pharma SpA
(Italy; Nuovo
Mercato:NOV)

BBR 3464

Novel tri-platinum complex

Ovarian and non-small-cell lung cancer

Phase II results showed that some patients experienced responses and other signs of biological activity (10/22)

OSI Pharma-
ceuticals Inc.
(OSIP)

Tarceva (OSI-774)

Epidermal growth factor receptor tyrosine kinase

Metastasized pancreatic cancer and refractory non-small-cell lung cancer

Company began two more Phase III trials (10/24)

Oxford
Biomedica
plc
(UK)*

TroVax

Gene-based therapeutic vaccine designed to stimulate a patient's immune system

Colorectal cancer

Phase I/II results showed the drug to be safe and well tolerated, and vaccine induced an immune response against the tumor antigen OBA1 in colorectal cancer (10/15)

OxiGene
Inc.
(OXGN)

CA4P

Combretastatin A4 prodrug; vascular targeting drug

Tumors

Phase I data showed statistically significant results demonstrating CA4P's ability to successfully reduce blood flow that feeds malignant tumors (10/31)

Protein
Design
Labs Inc.
(PDLI)

Remitogen

SMART 1D10, apolizumab; humanized antibody

Non-Hodgkin's lymphoma or chronic lymphocytic leukemia

Company initiated a Phase I trial testing Remitogen in combination with IDEC Pharmaceutical Corp.'s Rituxan (10/29)

Slil Biomed-
ical
Corp.*

SL11047

Second-generation polyamine analogue

AIDS-lymphoma

Company will begin a Phase I trial (10/23)

Sonus Pharma-
ceuticals
Inc.
(SNUS)

S-8184

Paclitaxel cancer product that used the company's vitamin E-based Tocosol delivery technology

Cancer

Phase I data indicate S-8184 can be given safely as a rapid injection and is well tolerated at higher doses than normally used with existing paclitaxel formulations (10/30)

Telik Inc.
(TELK)

TLK286

Small-molecule drug that targets tumors that over-express GST P1-1

Colorectal, ovarian and non-small-cell lung cancer

Phase II data show TLK286 produces apoptosis in a concentration- and time-dependent manner (10/31)

Transgene
SA
(France;
TRGNY)

MVA-HPV-
IL2

Anticancer vaccine; associates a pox virus vector derived from the modified virus ankara strain with antigens of the human papillomavirus type 16

Cervical cancer

Company initiated a Phase II trial (10/18)

CARDIOVASCULAR

Alliance
Pharmaceu-
tical Corp.
(ALLP)

Oxygent

Perflubron emulsion

Cardiopulmonary bypass

Phase III cardiac surgery study results demonstrated oxygenation benefits (10/19)

Alteon Inc.
(AMEX:ALT)

ALT-711

Orally active drug designed to reverse cardiovascular disease

Systolic hyper- tension and left ventricular hypertrophy

Company initiated a second Phase IIb (10/23)

Centocor Inc.
(a Johnson
& Johnson
company)

Remicade
(FDA-
approved)

Infliximab; chimeric monoclonal antibody to tumor necrosis factor-alpha

Advanced congestive heart failure

Company placed a hold on further development based on Phase II results that showed there was no improvement in a patient's clinical status and a higher incidence of mortality and hospitalization (10/22)

Esperion
Therapeu-
tics Inc.
(ESPR)

ETC-642

RLT Peptide product candidate

Cardiovascular disease

Company received approval to begin a Phase I trial (10/9)

Texas Bio-
technology
Corp.
(TXBI)
and Glaxo-
Smith-Kline
plc
(UK)

Argatroban
(FDA-
approved)

Anticoagulant therapy; synthetic direct thrombin inhibitor that blocks the activity of thrombin

For patients undergoing percutaneous coronary interventions

Companies initiated a Phase II trial (10/9)

CENTRAL NERVOUS SYSTEM

AtheroGenics
Inc.
(AGIX)

AGIX-4207

Intravenous treatment; small-molecule drug from AtheroGenics' v-protectant technology; a selective modulator of TNF-alpha- induced redox-sensitive inflammatory genes

Rheumatoid
arthritis

Company initiated a Phase I trial (10/2); company completed the escalating single-dose segment of the Phase I trial (10/23)

Axonyx Inc.
(AXYX)

Phenserine

Acetylcholinesterase
inhibitor

Alzheimer's disease

Company reported positive safety and efficacy results from a Phase II study (10/30)

Cellegy
Pharma-
ceuticals
Inc.
(CLGY)

Nitroglycerin

Nitroglycerin ointment

Genital pain caused by vulvadynia

All 12 patients in a study were relieved of pain within five minutes following application of the ointment; six women had a significant reduction of pain during sexual activity; the ointment was well tolerated, but most women experienced headaches (10/25)

Genmab A/S
(Denmark;
CSE:GEN)

HuMax-IL15

Fully human antibody

Active rheumatoid arthritis

Company initiated a Phase I/II trial (10/3)

Pain Thera-
peutics
Inc.
(PTIE)

PTI-555

Morphine

Moderate to severe pain

Phase II results showed the primary endpoint of pain relief was achieved (10/4)

United Thera-
peutics
Corp.
(UTHR)

Beraprost

Oral therapeutic; form of prostacyclin, which is produced in blood vessels to keep them dilated and free of platelet aggregation

Intermittent claudication (pain while walking)

Beraprost failed to meet endpoints in peripheral vascular disease patients with intermittent claudication; the company is abandoning development plans (10/15)

DIABETES

Generex
Biotech-
nology
Corp.
(Canada;
GNBT)

Oralin

Oral insulin formulation

Type I and Type II diabetes

Clinical data indicate that Oralin can be used safely and effectively in place of injected insulin (10/22)

INFECTION

Cel-Sci Corp.
(AMEX:CVM)

Multikine

Immunotherapy drug; natural mixture of human cytokines, including interleukin-2

HIV and human papillomavirus- induced cervical dysplasia

Clinical data showed that all five women treated showed clinical improvement (10/9); Phase I results showed six of eight patients had no evidence of dysplasia on biopsy seven to eight weeks after final injection (10/30)

Cerus Corp.
(CERS) and
Baxter Health-
care Corp.

Intercept Red Blood Cell System

Pathogen inactivation
system

To protect against infectious diseases transmitted through red blood cell transfusions

Phase Ic results showed that the mean survival of the Intercept cells were 62.2 days, which is not statistically different from the 61.1 days of survival of untreated red blood cells (10/17)

Cubist Pharma-
ceuticals
Inc.
(CBST)

Cidecin

Daptomycin for injection

Skin and soft-tissue infections

Cidecin achieved its primary endpoint in a second pivotal trial (10/4); the company expects to file for regulatory approval in mid-2002 (10/26)

DepoMed
Inc.
(AMEX:
DMI)

Ciprofloxacin
GR

Antibiotic delivered with DepoMed's Gastric Retention System

Urinary tract infections

Company initiated a Phase II trial (10/1)

Enzo Biochem
Inc.
(NYSE:
ENZ)

EHT899

Orally available viral protein

Chronic active hepatitis associated with hepatitis B

Phase II results indicate that the 42 individuals treated showed improvement in key areas of liver inflammation (10/12)

Hollis-Eden
Pharmaceu-
ticals Inc.
(HEPH)

HE2000

Immune-regulating hormone

Hepatitis B

Company received approval to initiate a Phase II trial (10/4)

Inhale
Therapeutic
Systems Inc.
(INHL)

Inhaleable tobramycin

An anti-infective drug; powdered tobramycin developed with Inhale's Inhance pulmonary delivery technology

Lung infections

Clinical results showed it was superior to nebulization when measuring delivery efficiency and lung deposition (10/2)

IntraBiotics
Pharmaceu-
ticals
Inc.
(IBPI)

Iseganan hydrochloride

Oral solution

Ventilator- associated pneumonia

Phase IIa results showed a 10-fold decrease in the mean oral microbial burden compared with negligible reductions in patients receiving placebo (10/4)

MedImmune
Inc.
(MEDI)

Synagis (FDA-
approved)

Palivizumab; binds to fusion protein on viral surface

Respiratory syncytial virus

Data confirm that Synagis reduces the rate of RSV-related hospitalization among high-risk infants (10/22)

Nexell Thera-
peutics Inc.
(NEXL)

¿

Hematopoietic stem cells

Chronic granulomatous disease

Company began patient enrollment in a Phase III trial (10/22)

Ribozyme
Pharmaceu-
ticals Inc.
(RZYM)

Heptazyme

Anti-hepatitis C ribozyme

Hepatitis C

Company began a Phase II trial (10/8)

Xenova
Group
plc
(UK; LSE:
XEN) and
GlaxoSmith-
Kline
plc (UK)

TA-HSV

Vaccine

Genital herpes

The Phase II trial failed to meet its clinical endpoints; company decided to drop development for this indication (10/10)

Xenova
Group
plc
(UK; LSE:XEN)

TA-HPV

Vaccine

High-grade vulval intraepithelial neoplasia

Phase IIa results showed the vaccine was safe and well tolerated (10/26)

Xenova
Group
plc
(UK; LSE:XEN)

TA-CIN

Vaccine

Cervical intraepithelial neoplasia

Phase I results showed TA-CIN was well tolerated (10/26)

MISCELLANEOUS

Advanced
Tissue
Sciences
Inc.
(ATIS)

¿

Human-based tissue; fibroblast cells grown on a bioabsorbable scaffold

Damaged gum tissue

In a study of more than 20 patients, Advanced Tissue's product demonstrated equivalence to autologous palatal grafts (10/9)

Amgen Inc.
(AMGN)

Aranesp (FDA-
approved)

Darbepoetin alfa

Chronic renal
failure

Clinical data from a study in which Aranesp was dosed once every four weeks showed 86% of patients with chronic renal failure receiving dialysis maintained hemoglobin levels within the study target range (10/16)

AnorMED
Inc.
(Canada;
TSE:AOM)

Foznol

Lanthanum carbonate

Hyperphospha-
taemia

Phase III results showed Foznol was able to maintain and control blood phosphate levels in patients (10/16)

Atrix Lab-
oratories
Inc.
(ATRX)

Atrisone

Dapsone topical gel in SMP technology

Acne

Company completed enrollment in a Phase III study (10/15)

Avigen Inc.
(AVGN)

Coagulin-B

Gene therapy

Hemophilia B

Company temporarily stopped the Phase I/II trial because trace amounts of the vector were found in the patient's semen (10/8)

Cellegy
Pharma-
ceuticals
Inc.
(CLGY)

Anogesic

Nitroglycerin ointment

Anal fissures

Phase III results support results of an earlier Phase III in which pain reduction was observed (10/2)

Cephalon
Inc.
(CEPH)

Provigil (FDA-
approved)

Modafinil

Excessive daytime sleepiness

Phase III data showed that Provigil helped keep people awake (10/9)

D-Pharm
Ltd.
(Israel)*
and Shire
Pharmaceu-
ticals Group
plc
(UK)

SPD 421

Phospholipid derivative of valproic acid

Epilepsy

Companies initiated Phase II trials (10/15)

Dusa Pharma-
ceuticals Inc.
(DUSA)

Levulan

Photodynamic therapy

Barrett's
esophagus

Company initiated its second Phase I/II trial (10/10)

Genaissance
Pharmaceu-
ticals
Inc.
(GNSC)

¿

Statin response examined by genetic HAP markers

To lower cholesterol

Company initiated its second clinical study designed to link human gene variation to clinical response in order to develop diagnostic and therapeutic products (10/18)

Human
Genome
Sciences Inc.
(HGSI)

Repifermin

Systemically administered treatment

Ulcerative colitis

Company completed enrollment in a Phase IIa trial (10/29)

InKine Pharm-
aceutical
Co. Inc.
(INKP)

Visicol (FDA-
approved)

Tablet form (formerly
Diacol)

Bowel cleansing prior to colonoscopy

Data from a 98-patient trial showed that Visicol is effective using fewer tablets and a reduced volume of clear liquid (10/23)

IntraBiotics
Pharmaceu-
ticals
Inc.
(IBPI)

Iseganan
hydrochloride

Formerly called Protegrin IB-367 Rinse; synthetically derived analogue of naturally occurring protegrins

Cystic fibrosis

Phase I safety data indicate that iseganan can be safely inhaled for up to three days (10/30)

Isis Pharma-
ceuticals
Inc.
(ISIP)

ISIS 2302

Antisense inhibitor of intercellular adhesion molecule-1

Active distal ulcerative colitis

Phase II data demonstrated improved symptoms in patients (10/10)

Lilly ICOS
LLC
(joint
venture of
ICOS Corp.
[ICOS] and Eli
Lilly & Co.)

Cialis

Oral treatment; a PDE5 inhibitor

Erectile
dysfunction

Phase III data showed that 81% of patients treated with 20 mg of Cialis reported improved erections; absorption was not decreased by food intake (10/2)

MediGene
AG
(Germany)*

Polyphenon E

Cream; anti-inflammatory that blocks virus binding to the cell

Genital warts

In a Phase III trial, the drug had a clearance rate of 61% for men and 57% for women, while placebo showed a 37% clearance (10/24**)

Modex
Therapeutics
Ltd.
(Switzerland;
SWX:MDXN)

EpiDex

Skin replacement product

Skin ulcers

Phase II data showed that 33% of patients displayed complete wound closure after 12 weeks (10/17**)

Nastech
Pharmaceu-
tical
Company
Inc.
(NSTK)

Somatropin

Recombinant human growth hormone

Growth failure

Company began a Phase I trial to evaluate the nasal administration of somatropin (10/4)

Neurocrine
Biosciences
Inc.
(NBIX)

NBI-34060

Type 1 GABA-a, a receptor agonist; chemically distinct from benzodiazepines

Transient
insomnia

Phase II results showed the drug achieved primary and secondary endpoints (10/1)

Oculex
Pharmaceu-
ticals Inc.*

Posurdex

Biodegradable microsized drug delivery system designed to provide continuous drug therapy for about one month inside the eye

Persistent macular edema

Company began to enroll patients in its Phase II trial (10/30)

Ortec Inter-
national
Inc.
(ORTC)

Orcel (FDA-
approved)

Cyropreserved form; bilayered cellular matrix

Venous leg ulcer

A preliminary review of the first 13 patients completing the trial indicated that nine patients achieved 100% wound closure in 12 weeks (10/31)

Progenics
Pharmaceu-
ticals
Inc.
(PGNX)

MNTX

Methylnaltrexone

Debilitating side effects of opioid pain medications

Phase II results showed MNTX significantly reduced the morphine-induced delay in mean oral-cecal transit time to near baseline rates (10/16)

Proneuron
Biotechnol-
ogies Ltd.
(Israel)*

¿

Autologous activated macrophage therapy for nerve regeneration

Spinal cord injury

Company initiated a second Phase I trial (10/22)

Protein
Design
Labs
Inc.
(PDLI)

¿

Humanized antibody to interleukin-4

Asthma

Company started a Phase II trial (10/9)

SangStat
Medical Corp.
(SANG)

ABX-CBL

Anti-CD147 monoclonal antibody

Steroid-resistant graft-vs.-host disease

Patients receiving at least four infusions demonstrated a complete or partial response in a Phase II study (10/4)

Transkary-
otic
Therapies
Inc.
(TKTX)

Replagal

Enzyme replacement therapy

Fabry's disease

Results from an open-label extension of a six-month pivotal trial showed Replagal was well tolerated, had an excellent safety profile and could have broad therapeutic effects (10/16)

Unigene
Laboratories
Inc.
(UGNE)

¿

Nasal calcitonin spray

Bone loss

Pivotal results showed a rapid and persistent reduction in bone loss as measured by several blood markers (10/9)


Notes:

* Privately held; ** Denotes the date the item ran in BioWorld International.

Unless otherwise noted, the stock symbols listed for public companies are on the Nasdaq market.

AMEX = American Stock Exchange; CSE = Copenhagen Stock Exchange; LSE = London Stock Exchange; NYSE = New York Stock Exchange; SWX = Swiss Stock Exchange; TSE = Toronto Stock Exchange