Company*
(Country;
Symbol)

Product

Description

Indication

Status
(Date)


AUTOIMMUNE

La Jolla
Pharmaceutical
Co.
(LJPC)

Riquent

Abetimus sodium; B-cell toleragen; designed to reduce levels of antibodies to double-stranded DNA

Lupus

The FDA, which had issued an approvable letter in October calling for more trials, said the drug was unlikely to gain accelerated approval (3/14)

CANCER

Advanced
Magnetics Inc.
(AMEX:AVM) and
Cytogen Corp.
(CYTO)

Combidex

Molecular imaging agent

Cancer diagnosis

An FDA advisory panel voted 15-4 against recommending approval for differentiating metastatic from non-metastatic lymph nodes across all cancer types (3/3)

Gamida-Cell
Ltd.*
(Israel)

StemEx

Ex vivo expanded cord blood stem/progenitor cells with non- expanded cells from the same unit

Advanced hematologic malignancies

The FDA granted orphan designation to the product for use as hematopoietic support in patients receiving high-dose therapy (3/15)

Genta Inc.
(GNTA)

LR3001

Antisense compound directed against the oncogene c-myb

Chronic myelocytic leukemia

The FDA designated orphan status to the drug, which has been tested in two Phase I trials (3/15)

Millennium
Pharmaceuticals
Inc.
(MLNM)

Velcade (FDA-approved)

Bortezomib; proteasome inhibitor

Multiple myeloma

The FDA approved supplemental NDA to include the treatment of patients who have received at least one prior therapy (3/25)

CARDIOVASCULAR

Inotek
Pharmaceuticals
Corp.*

INO-1001

Inhibitor of the nuclear cell death enzyme poly (ADP- ribose) polymerase

Aortic aneurysm repair

Reached agreement with FDA on SPA for pivotal trial for reducing complications associated with thoracoabdominal aortic aneurysm repair surgery (3/3)

CENTRAL NERVOUS SYSTEM

Cephalon
Inc.
(CEPH)

Nuvigil

Armodafinil; single isomer of the active ingredient in Provigil (modafinil)

Excessive sleepiness

Filed NDA with FDA seeking approval for improving wakefulness associated with narcolepsy, shift-work sleep disorder and obstructive sleep apnea/hypopnea syndrome (3/31)

Cephalon
Inc.
(CEPH)

Actiq (FDA-approved)

Oral transmucosal fentanyl citrate; sugar-free formulation

Pain in cancer patients

The FDA issued an approvable letter on the new formulation; Cephalon said it expects a 3Q:05 approval (3/25)

Orphan
Medical Inc.
(ORPH)

Xyrem (FDA-approved)

Sodium oxybate oral solution

Narcolepsy

The FDA accepted the supplemental NDA filing; the review deadline is Nov. 18, 2005 (3/21)

DIABETES

Amylin
Pharmaceuticals
Inc.
(AMLN)

Symlin

Pramlintide acetate; an analogue of human amylin

Types I and II diabetes

The FDA approved the drug for use with insulin in patients who failed to achieve desired glucose control with insulin (3/16)

Depomed Inc.
(DEPO) and
Biovail Corp.
(Canada)

Glumetza

Once-daily, extended-
release formulation of
metformin hydrochloride

Type II diabetes

The FDA issued an approvable letter saying the drug is approvable pending the completion of discussions related to one manufacturing specification (3/1)

Keryx Bio-
pharmaceuticals
Inc.
(KERX)

KRX-101

Sulodexidel; oral heparinoid compound

Diabetic nephropathy

Finalized SPA with the FDA on Phase III and IV trials; a single Phase III trial will be run in patients with microalbuminuria (3/16)

INFECTION

ID Biomedical
Corp.
(Canada;
IDBE)

Fluviral

Influenza vaccine

Influenza

The FDA said the product is eligible for accelerated approval and priority review, meaning it is possible it could be licensed for the 2006-07 season (3/15)

Theravance
Inc.
(THRX)

Telavancin

Lipoglycopeptide antibiotic believed to have multiple mechanisms of action

Hospital- acquired pneumonia and complicated skin and skin-structure infections

The FDA granted fast-track designation to the Phase III drug in HAP and complicated skin and complicated skin and skin-structure infections (3/28)

MISCELLANEOUS

Halozyme
Therapeutics
Inc.
(AMEX:HTI)

Enhanze SC

Formulation of recombinant human hyaluronidase

For use as a spreading agent

The company filed an NDA with the FDA (3/28)

Insmed Inc.
(INSM)

SomatoKine

Composition of insulin-like growth factor-1 and its primary binding protein, BP3

Growth hormone insensitivity syndrome

The FDA accepted for review the NDA on the orphan drug, which was filed in January (3/10)

ISTA
Pharmaceuticals
Inc.
(ISTA)

Xibrom

Bromfenac sodium solution; topical non-steroidal anti-inflammatory agent

Ocular inflammation following cataract surgery

The FDA approved the product; launch is expected in the second quarter (3/28)

PTC
Therapeutics
Inc.*

PTC124

Oral agent that targets nonsense mutations

Cystic fibrosis

The FDA granted fast-track designation to the product in that indication (3/31)


Notes:

* Privately held.

BLA = Biologics license application; CMA = Continuous marketing application; FDA = Food and Drug Administration; IND = Investigational new drug application; NDA = New drug application; SPA = Special protocol assessment.

Unless otherwise noted, the stock symbols listed for public companies are on the Nasdaq market.

AMEX = American Stock Exchange.