Data reported from first-in-human ATB200-02 trial of ATB-200/AT-2221 combination in Pompe disease July 3, 2019
Dicerna to initiate clinical development of DCR-A1AT for A1AT deficiency-associated liver disease July 3, 2019
Topline data released from phase IIa study of gemcabene in familial partial lipodystrophy June 27, 2019
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