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BioWorld - Wednesday, January 14, 2026
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Home » Oh, Skip It? FDA View Changing; Sarepta’s DMD Efforts Hit Hard
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Oh, Skip It? FDA View Changing; Sarepta’s DMD Efforts Hit Hard

Nov. 13, 2013
By Randy Osborne
The FDA altered its view of Sarepta Therapeutics Inc.’s data with exon-skipping therapy eteplirsen for Duchenne muscular dystrophy (DMD) after Prosensa Holding NV’s failure with exon-skipper drisapersen for the condition, but Sarepta CEO Chris Garabedian hopes the agency can still be brought around.
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