Company*

(Country; Symbol)

Product

Description

Indication

Status

(Date)


AUTOIMMUNE

Abbott Laboratories (NYSE:ABT)

ABT-874

Designed to selectively inhibit proteins such as pro-inflammatory interleukins or tumor necrosis factor-alpha

Psoriasis

Phase II data demonstrated significantly reduced psoriasis symptoms in the majority of patients treated (5/4)

Alba Therapeutics Corp.*

AT-1001

Orally administered zonulin receptor antagonist

Celiac disease

Phase IIa data showed dose-dependent responses were seen in intestinal permeability, and that drug patients had improved symptoms and outcomes (5/7)

Amgen Inc. (AMGN) and Wyeth

Enbrel (FDA-approved)

Etanercept; antitumor necrosis factor-alpha antibody

Nail psoriasis

Patients showed reduced severity by more than 28% at 12 weeks and reduced signs and symptoms (5/18)

Celgene Corp. (CELG)

CC-10004

Apremilast; oral TNF antagonist

Psoriasis

Phase II data showed it achieved its primary endpoint after 12 weeks of treatment (5/22)

ChemoCentryx Inc.*

Traficet-EN

An oral, anti-inflammatory agent designed to target the CCR9 receptor

Crohn's disease

Phase II data showed the product is well tolerated and had clinical activity (5/24)

Cytos Biotechnology AG (Switzerland; SWX:CYTN)

CYT007-TNFQb

Vaccine candidate

Psoriasis

Phase I/IIa data showed it was safe and well tolerated (5/24)

Enzo Biochem Inc. (NYSE:ENZ)

Alequel

An oral immune regulation preparation consisting of an autologous protein-containing extract prepared from mucosal tissue colon biopsies of the subject

Crohn's disease

Interim Phase II data suggested the approach induced clinical remissions and improved patients' quality of life compared to placebo (5/22)

Human Genome Sciences Inc. (HGSI)

LymphoStat-B

Belimumab; human monoclonal antibody that inhibits activity of B-lymphocyte

Systemic lupus erythematosus

Began the second of two pivotal Phase III trials (5/30)

La Jolla Pharmaceutical Co. (LJPC)

Riquent

Abetimus sodium; B-cell toleragen

Systemic erythematosus lupus

Phase III data showed a dose response in the 100 mg, 300 mg and 900 mg groups, with the reductions in median antibody levels between Riquent and placebo at week eight of 30%, 40% and 58% (5/24)

Targeted Genetics Corp. (TGEN)

tgAAC94

Therapy that uses an adeno-associated viral vector to deliver a soluble TNF-alpha receptor protein

Inflammatory arthritis

Achieved the enrollment target of 120 patients in a Phase I/II trial (5/24)

CANCER

Alchemia Ltd. (Australia; ASX:ACL)

HyCAMP

Formulation of the anticancer drug irinotecan

Metastatic colorectal cancer

Phase II data demonstrated superior anticancer activity compared to Camptosar (irinotecan), with a significantly greater number of patients with observed tumor responses (5/29)

Amgen Inc. (AMGN)

Vectibix (FDA-approved)

Panitumumab; fully human monoclonal antibody directed against the epidermal growth factor receptor

Metastatic colorectal cancer

Phase III showed it prolonged progression-free survival compared to best supportive care (5/1)

Antigenics Inc. (AGEN)

Oncophage

Vitespen; cancer vaccine

Cancer

Phase III data showed a clinically significant improvement in recurrence-free survival of about 45% (5/21)

Array BioPharma Inc. (ARRY)

ARRY-520

A small molecule, kinesin spindle protein inhibitor

Cancer

Started a Phase I trial (5/3)

BioDelivery Sciences International Inc. (BDSI)

BEMA Fentanyl

Consists of a small, dissolvable polymer disc formulated with the opioid narcotic fentanyl

Cancer patients with break-through pain

Phase III data showed the product demonstrated statistical significance vs. placebo on a summary of pain at 15 minutes, a secondary endpoint (5/14)

Celgene Corp. (CELG)

Revlimid (FDA-approved)

Lenalidomide

Multiple myeloma

Closed enrollment in a Phase III study comparing dexamethasone with a combined therapy of dexamethasone and Revlimid (5/16)

Celldex Therapeutics Inc. *

CDX-110

Peptide vaccine

Glioblastoma multiforme

Began a Phase II/III trial (5/24)

Cell Genesys Inc. (CEGE)

GVAX

Immunotherapy comprised of a single leukemia cancer cell line modified to secrete GM-CSF

Chronic myelogenous leukemia

Started three trials with the Johns Hopkins Sidney Kimmel Cancer Center (5/9)

Cel-Sci Corp. (AMEX:CVM)

Multikine

Mixture of human cytokines designed to stimulate an immune response

Head and neck cancer

Multikine significantly increased long term overall survival in a Phase II study (5/21)

Cougar Biotechnology Inc. (OTC BB:CGRB)

CB7630

Abiraterone acetate; oral, irreversible CYP450c17 enzyme inhibitor

Prostate cancer

Phase I and Phase II data showed it was well tolerated at doses as high as 2,000 mg/day with minimal toxicity; they also showed that 60% of patients experienced a confirmed decline in prostate specific antigen levels of greater than 50% (5/22)

CuraGen Corp. (CRGN) and TopoTarget A/S (Denmark; CSE:TOPO)

PXD101

Intravenous belinostat, an HDAC inhibitor

Soft tissue sarcomas

Started a Phase I/II clinical trial (5/2)

Cytogen Corp. (CYTO)

Prostascint

Capromab pendetide; brachytherapy; monoclonal antibody that targets prostate specific membrane antigen, conjugated with indium 111

Prostate cancer

Data from a large cohort study demonstrated the value of the imaging product in predicting prognosis in prostate cancer (5/22)

Dendreon Corp. (DNDN)

Provenge

Sipuleucel-T; active cellular immunotherapy

Prostate cancer

Phase III data showed a prolonged survival benefit for patients first treated with Provenge who then went on to receive docetaxel after disease progression (5/21)

EntreMed Inc. (ENMD)

Panzem NCD

2-methoxyestradiol; designed to work by attacking tumor cells through multiple mechanisms

Recurrent glioblastoma multiforme

Started a Phase II combination study with Panzem NCD and Temodor (5/29)

Exelixis Inc. (EXEL)

XL647

Designed to inhibit the activity of multiple receptor tyrosine kinases

Non-small-cell lung cancer

Began a Phase II trial (5/30)

Gemin X Biotechnologies Inc.*

GMX1777

A water-soluble, intravenously administered prodrug of LEO's CHS828

Refractory solid tumors and lymphomas

Began a Phase I trial (5/8)

Generex Biotechnology Corp. (GNBT)

AE37

Immunotherapeutic vaccine

Breast cancer

First patients have been treated in a Phase II trial

Genitope Corp. (GTOP)

MyVax

Personalized immunotherapy

Follicular non-Hodgkin's lymphoma

Started a Phase II trial (5/21)

ImmunoCellular Therapeutics Ltd. (OTC BB:IMUC)

A dendritic cell-based vaccine product

Brain tumors

Began a Phase I trial (5/11)

Innate Pharma SA (France; PARIS:IPH)

IPH 1101

Immunomodulator that activates non-conventional T-lymphocytes

Non-Hodgkin's lymphoma

Started a clinical trial (5/2)**

Inovio Biomedical Corp. (AMEX:INO)

DNA vaccine delivered using Inovio's electro-poration approach

Prostate cancer and melanoma

Phase I/II data indicated that the delivery system was safe and well tolerated (5/22 and 5/24)

Introgen Therapeutics Inc. (INGN)

Advexin

Adenoviral vector containing the p53 tumor suppressor gene

Li-Fraumeni Syndrome

Clinical data showed a benefit in one patient with the rare, inherited form of cancer (5/30)

Mersana Therapeutics Inc.*

XMT-1001

Fleximer-based product that uses a dual-release mechanism to liberate a camptothecin prodrug, which is converted within cells into camptothecin

Solid tumors

Began a Phase I trial (5/30)

Molecular Insight Pharmaceuticals Inc.*

Azedra (formerly Ultratrace MIBG)

Radiopharmaceutical designed to maximize delivery of MIBG molecules

Malignant pheochromocytoma

Started a Phase I/II trial (5/10)

Ortho Biotech Products LP

Doxil (FDA-approved)

Liposomal formulation of doxorubicin

Multiple myeloma

FDA approved the use of Doxil with Velcade (Millennium Pharmaceuticals Inc.) to treat patients who have not received Velcade previously but have received one prior therapy (5/21)

Peregrine Pharmaceuticals Inc. (PPHM)

Bavituximab

A monoclonal antibody designed to target and bind to phophatidylserine

Advanced cancer

Phase Ib data showed that 50% of all evaluable patients achieved objective tumor response or stable disease, and 75% receiving the therapy combined with gemcitabine achieved objective tumor response or stable disease (5/31)

Poniard Pharmaceuticals Inc. (PARD)

Picoplatin

New-generation platinum therapy

Small-cell lung cancer

Began a pivotal Phase III trial (5/1)

Pro-Pharmaceuticals Inc. (AMEX:PRW)

Davanat

Carboyhdrate compound designed for targeted delivery

Chemotherapy-sensitive colorectal cancer

Stabilized disease was seen in seven of eight patients in a Phase II trial (5/14)

Protherics plc (UK; PTIL)

OncoGel

Sustained-release formulation of paclitaxel

Esophageal cancer

Phase IIa data showed that OncoGel improved dysphagia symptoms in nine patients (5/22)

Rexahn Pharmaceuticals Inc. (OTC BB:RXHN)

Archexin

First-in-class signal inhibitor that directly blocks the production of AKT

Renal cell carcinoma

Is beginning a Phase II trial (5/30)

Serenex Inc.*

SNX-5422

A heat-shock protein 90 inhibitor; orally administered small molecule

Cancer

Started a Phase I trial (5/31)

Spectrum Pharmaceuticals Inc. (SPPI)

EOquin

Apaziquone for intravesical instillation; activated by reductase enzymes found in cancer cells

Non-invasive bladder cancer

Started its pivotal Phase III trials (5/2)

Spectrum Pharmaceuticals Inc. (SPPI)

Satraplatin

Oral platinum compound

Hormone-refractory prostate cancer

Phase III data showed a median time to pain progression of 66.1 weeks for the satraplatin arm compared to 22.3 weeks for placebo (5/22)

Tapestry Pharmaceuticals Inc. (TPPH)

TPI 287

A next-generation taxane

Hormone-refractory prostate cancer

Started enrolling patients in a Phase II trial (5/9)

Vion Pharmaceuticals Inc. (VION)

Cloretazine

VNP40101M; small-molecule alkylating agent that is designed to work by damaging DNA by releasing the chloro-ethylating agent 90CE into the blood stream

Relapsed adult myelogenous leukemia

Vion suspended enrollment and further patient treatment pending a review of all data based on a recommendation of a data safety monitoring board (5/23)

Viventia Biotech Inc.* (Canada)

Vicinium

Armed antibody administered using intravesical instillation

Bladder cancer

Phase I/II data showed it was well tolerated at all dose levels with no maximum tolerated dose reached (5/25)

Ziopharm Oncology Inc. (ZIOP)

ZIO-101

Organic arsenic

Primary liver cancer

Dosed the first patient in a Phase II trial (5/10)

CARDIOVASCULAR

Acusphere Inc. (ACUS)

Imagify

Perflubutane polymer microspheres

Coronary artery disease

Phase III failed to achieve end-point but exceeded the criteria for success on accuracy and sensitivity (5/1)

Alliance Pharmaceutical Corp. (OTC BB:ALLP)

Oxygent

Perfluorochemical emulsion

To prevent postoperative ileus resulting from hypoxia during major surgery

Is starting a Phase IIb trial with 128 patients (5/16)

BioMarin Pharmaceutical Inc. (BMRN)

6R-BH4

Sapropterin dihydrochloride

Sickle cell disease

Started treatment in a Phase IIa trial (5/2)

Cardium Therapeutics Inc. (OTC BB:CDTP)

Generx

Alferminogen tadenovec, Ad5FGf-4

Myocardial ischemia

Started recruiting female patients for a Phase III trial (5/16)

Celladon Corp.* and Targeted Genetics Corp. (TGEN)

Mydicar

Uses an adeno-associated virus vector to deliver the SERCA2a gene to heart muscle tissue

Heart failure

Started a Phase I trial (5/16)

Danube Pharmaceuticals Inc.*

DNB-001

A first-in-class oral therapy with dual potent IOP-reducing and tissue protective effects

Ocular hypertension

Started a Phase II study in 60 patients (5/16)

DeCODE genetics Inc. (Iceland; DCGN)

DG051

Small-molecule inhibitor of leukotriene A4 hydrolase

To prevent heart attacks

Phase I data showed it reduced leukotriene B4 production in a dose-dependent manner (5/1)

Discovery Laboratories Inc. (DSCO)

Surfaxin

Engineered version of natural human lung surfactant

Respiratory distress syndrome

One-year follow-up of Phase III trials showed that Surfaxin had a statistically significant survival advantage in premature infants compared to existing animal-derived surfactants (5/31)

Dyax Corp. (DYAX)

DX-88

Ecallantide; a recombinant small protein shown to inhibit human plasma kallikrein

To prevent blood loss during cardiothoracic surgery

Began patient treatment in the Phase II trial (5/14)

Gilead Sciences Inc. (GILD)

Ambrisentan

An endothelin receptor antagonist

Pulmonary arterial hypertension

Long-term data showed that improvements in six-minute walk distance observed during the first 12 weeks of treatment were sustained for at least 48 weeks and the one-year probability of survival was 95% (5/21)

InterMune Inc. (ITMN)

Pirfenidone

Small-molecule p38-gamma inhibitor

Idiopathic pulmonary fibrosis

Completed patient enrollment in CAPACITY, a Phase III trial (5/16)

Isis Pharmaceuticals Inc. (ISIS)

ISIS 301012

Second-generation antisense drug designed to inhibit apoE-100

Homozygous familial hypercholesteremia

Phase II data showed that three patients who completed 12 weeks of treatment at 300 mg/week achieved 45%, 50% and 51% additional reductions in LDL-cholesterol beyond that achieved with lipid-lowering therapy (5/16)

Kai Pharmaceuticals Inc.*

KAI-1455

A selective epsilon protein kinase C activator

To reduce ischemic injury during planned surgical procedures

Began dosing subjects in a Phase I trial (5/4)

Medicure Inc. (Canada; AMEX:MCU)

MC-1

Naturally occurring small molecule that protects cardiomyocytes

To reduce ischemic reperfusion injury

Phase II data demonstrated a statistically significant lower incidence of atrial fibrillation in the MC-1 groups compared to placebo between postoperative day four and the end of the trial (5/31)

Momenta Pharmaceuticals Inc. (MNTA)

M118

A next-generation anticoagulant

Acute coronary syndromes

Started dosing in a Phase I study (5/14)

NicOx SA (France; FSE:NXO)

NCX 1000

Nitric oxide-donating derivative of ursodeoxycholic acid

Portal hypertension

Phase IIa data from 11 patients did not demonstrate the efficacy required to support continuation of the study; company is not pursuing further development (5/11)

Northfield Laboratories Inc. (NFLD)

PolyHeme

Oxygen-carrying blood substitute derived from human blood

Blood loss

Pivotal data showed it missed its dual primary efficacy endpoints of superiority and non-inferiority a month after injury, as well as its primary safety endpoint (5/23)

Pipex Pharmaceuticals Inc. (OTC BB:PPEX)

Coprexa

Oral tetrathiomolybdate

Refractory idiopathic pulmonary fibrosis

Phase I/II data were positive and has led to a 12-month, randomized, double-blind, placebo-controlled trial (5/25)

SkyePharma plc (UK; LSE:SKP) and Sciele Pharma Inc. (SCRX)

Sular

A calcium channel blocker that uses SkyePharma's Geomatrix technology

High blood pressure

Completed a clinical program that showed the new Sular formulation is bioequivalent to Sciele's currently marketed Sular (5/14)

Trigen Ltd.* (UK)

PR-15

A platelet adhesion inhibitor

To manage arterial thrombosis

Completed the first Phase I (5/1)

CENTRAL NERVOUS SYSTEM

Accera Inc.*

AC-1202

Orally available, liquid compound converted by the liver into ketone bodies

Alzheimer's disease

Phase IIb data showed that those who did not have the ApoE4 genotype responded particularly well to treatment (5/1)

Acorda Therapeutics Inc. (ACOR)

Fampridine-SR

A sustained-release tablet; selective neuronal potassium channel blocker

Multiple sclerosis

Phase III data showed the average increase in walking speed was 25.2% vs. 4.7% for the placebo group (5/3)

Active Biotech AB (Sweden; SSE:ACTI)

Laquinimod

Oral 0.6-mg dose; small molecule immunomodulatory agent

Multiple sclerosis

36-week Phase IIb data showed it significantly reduced MRI disease activity by 38% (5/1)

Anesiva Inc. (ANSV)

4975

Long-acting, non-opioid candidate

Postsurgical pain associated with total knee replacement

Phase II data showed a significant reduction in pain (5/1)

Avicena Group Inc. (OTC BB:AVGO)

AL-02

Neuroprotective agent

Amyotrophic lateral sclerosis

Started a Phase I study (5/14)

Biogen Idec Inc. (BIIB) and Vernalis plc (UK; LSE:VER)

BIIB014

An adenosine A2A receptor antagonist

Parkinson's disease

Began Phase II testing (5/8)

BioLineRx Ltd.* (Israel)

BL-1020

GABA-enhanced antipsychotic

Schizophrenia

Phase I data showed it was well tolerated and demonstrated biochemical evidence of dopamine blockade (5/22)

BioMS Medical Corp. (Canada; TSX:MS)

MBP8298

Synthetic peptide

Multiple sclerosis

Completed enrollment in its Phase II (5/3)

Cephalon Inc. (CEPH)

Fentora

Fentanyl buccal tablet

Breakthrough pain

Phase III trial showed it is beneficial (5/1)

Ceregene Inc.*

CERE-110

A gene therapy product designed to deliver nerve growth factor

Alzheimer's disease

Presented positive interim Phase I data showing it was well tolerated (5/3)

Durect Corp. (DRRX) and Voyager Pharmaceutical Corp.*

Memryte

Durin implant technology with leuprolide acetate

Alzheimer's disease

Phase III trial turned up positive outcome trends among women, but no positive effect among men (5/18)

EpiCept Corp. (EPCT)

EpiCept NP-1

Topical analgesic cream

Managing pain

Data showed it was safe and well tolerated in all age groups studied (5/3)

FoldRx Pharmaceuticals Inc.*

Fx-1006A

Small-molecule compound designed to inhibit the formation of amyloid deposits

Familial amyloid polyneuropathy

Started the Phase II/III study (5/29)

Genaera Corp. (GENR)

MSI-1436

Trodusquemine, an appetite suppressant

Obesity

Began enrolling patients in the first human study (5/7)

Genentech Inc. (NYSE:DNA) and Biogen Idec Inc. (BIIB)

Rituxan (FDA-approved)

Rituximab; antibody that targets and depletes CD20-positive B-cells

Multiple sclerosis

Phase II data showed the total number of gadolinium lesions was reduced in a statistically significant manner vs. placebo (p<0.0001) (5/1)

Medivation Inc. (MDVN)

Dimebon

Neuroprotectant agent that's been on the market in Russia since 1983

Alzheimer's disease

Six-month Phase II data showed that both subgroups improved vs. placebo on all five efficacy endpoints studied (5/4)

Neurogen Corp. (NRGN)

NG2-73

Selective modulator of gamma aminobutyric receptors

Insomnia

Phase I and Phase IIa data showed it rapidly induced sleep in a transient insomnia study (5/23)

Opexa Therapeutics Inc. (OPXA)

Tovaxin

A subcutaneous T-cell vaccine

Multiple sclerosis

Completed patient enrollment in a 150-patient Phase IIb study (5/17)

Pozen Inc. (POZN) and GlaxoSmithKline plc (UK)

Trexima

Single tablet containing sumatriptan 85 mg formulated with RT Technology and naproxen sodium 500 mg

Migraine

Showed significantly more patients using Trexima early in migraine attacks were pain-free at two hours (5/2)

Prestwick Pharmaceuticals Inc.*

Xenazine

Tetrabenazine; dopamine depletor that works by selectively blocking the VMAT2 transporter

Chorea associated with Huntington's disease

Clinical data showed Xenazine maintained reduction of chorea up to 80 weeks in patients who completed treatment in a 13-week trial (5/4)

Nabi Bio-pharmaceuticals (NABI)

NicVAX

Nicotine conjugate vaccine

Smoking cessation

NicVAX met its primary endpoint in an ongoing Phase IIb trial (5/2)

Neurogen Corp. (NRGN)

NGD-4715

Small molecule antagonist at the melanin concentrating hormone receptor-1

Obesity

Compound was safe and well tolerated at all doses in its first clinical trial (5/2)

Orexigen Therapeutics Inc. (OREX)

Contrave

A fixed-dose product that combines sustained-release formulations of bupropion and naltrexone

Obesity

Moved Contrave into the second of four Phase III studies (5/22)

Shire plc (UK)

Vyvanse (FDA-approved)

Lisdexamfetamine dimesylate

Attention deficit hyperactivity disorder

Phase III data showed that 95% of children taking Vyvanse daily for 12 months had overall improvement (5/24)

Synthetic Blood International Inc. (OTC BB: SYBD)

Oxycyte

An oxygen carrier, perfluorocarbon-based blood substitute and therapeutic oxygen carrier

Traumatic brain injury

Phase IIa data showed it met its primary endpoint of increasing patients' oxygen tension levels compared with baseline (5/15)

Vanda Pharmaceuticals Inc. (VNDA)

Iloperidone

5HT2/D2 antagonist

Schizophrenia

Phase III data showed it met its primary endpoint of improvement on the positive and negative symptom scale vs. placebo (5/25)

DIABETES

AtheroGenics Inc. (AGIX)

AGI-1067

Oral small molecule; an anti-oxidant

Diabetes

Plans to start a Phase III trial after a failed Phase III in atherosclerosis indicated encouraging data in Type II diabetes patients (5/31)

Cardium Therapeutics Inc. (OTC BB:CDTP)

Excellarate

A DNA-based collagen gel

Diabetic foot ulcers

Advancing Excellarate into a Phase IIb trial (5/1)

Biovitrum AB (Sweden; SSE:BVT)

BVT.115959

A2A agonist

Diabetic neuropathic pain

Started a Phase II trial (5/3)

Oculus Innovative Sciences Inc. (OCLS)

Dermacyn

Topical treatment; an oxychlorine formulation manufactured using Oculus' Microcyn technology

Diabetic foot infections

Began a 60-patient, randomized and open-label Phase II trial (5/21)

Trophos SA* (France)

TRO19622

Compound believed to promote the survival of a range of neurons

Diabetic neuropathy

Enrolled the first patients in its Phase IIa trial (5/16)

INFECTION

Amarillo Biosciences Inc. (OTC BB:AMAR) and CytoPharm Inc.* (Taiwan)

Interferon alpha

Oral human interferon alpha

Hepatitis C

Engaged a clinical research organization to conduct a clinical trial in 152 patients (5/31)

Avant Immunotherapeutics Inc. (AVAN)

Ty800

Vaccine against Salmonella typhi, the cause of typhoid fever

Typhoid fever

Phase I/II data showed the single-dose, oral vaccine was well tolerated and immunogenic (5/18)

Cytheris SA* (France)

CYT107

Recombinant interleukin

Hepatitis C and oncology

Plans to start two Phase I/IIa trials (5/31)

Innate Pharma SA (France; PARIS:IPH)

IPH 1101

Immunomodulator that activates non-conventional T-lymphocytes

Non-Hodgkin's lymphoma

Started a clinical trial (5/2)**

Intarcia Therapeutics Inc.*

Omega interferon

Injectable therapeutic; recombinant, glycosylated human type-1 interferon

Hepatitis C virus

Phase II data of the therapy with ribavirin compared to omega interferon alone showed the combination treatment is well tolerated and shows antiviral activity (5/21)

Iomai Corp. (IOMI)

Influenza vaccine patch; adjuvant called LT

Influenza

Phase I data showed the patch did not work as well as injected vaccine (5/25)

MedImmune Inc. (MEDI)

Numax

Motavizumab

To prevent respiratory syncytial virus

In a Phase III trial, Numax overall demonstrated 26% fewer RSV hospitalizations than Synagis (5/8)

NanoBio Corp.*

NB-002

Topical treatment

Onychomycosis

Phase I safety data was positive (5/22)

Nektar Therapeutics Inc. (NKTR)

NKTR-061

Inhaled Amikacin; developed using Nektar's micropump technology

Gram-negative pneumonia

Phase IIa data showed the use of aerosol antibiotics with systemic therapy might be effective in treating mechanically ventilated patients with hospital-acquired illness (5/21)

Optimer Pharmaceuticals Inc. (OPTR)

OPT-80

An RNA polymerase inhibitor

Clostridium difficile-associated diarrhea

Started another Phase III trial (5/1)

Pacgen Bio-pharmaceuticals Corp. (Canada; CDNX:PGA)

PAC-113

Peptide-based antifungal drug candidate

Oral Candida infection

Phase I/II data showed it was generally safe, well tolerated and active in the treatment of the infection (5/7)

Progenics Pharmaceuticals Inc. (PGNX)

PRO 140

A humanized monoclonal antibody that targets a distinct site on CCR5

HIV

First clinical trial showed patients receiving 5 mg/kg achieved an average maximum decrease of viral concentrations of 98.5% (5/1)

Sequella Inc.*

SQ109

An oral diamine antibiotic

Tuberculosis

Phase Ia data showed it was safe and well tolerated up to 300 mg (5/2)

Theratechnologies Inc. (Canada; TSX:TH)

TH9507

A stabilized analogue of the growth hormone-releasing factor

HIV-associated lipodystrophy

Completed 52 weeks of treatment in the first Phase III study (5/2)

Transport Pharmaceuticals Inc.*

SoloVir

Electrokinetic transdermal system with single-use drug cartridges containing Transport's acyclovir gel formulation

Cold sores

Began a Phase II trial (5/1)

VASTox plc (UK; LSE:VOX)

Neurodisorder drugs; small molecule candidates

Parkinson's disease symptoms

Phase I data showed they were safe and significantly suppressed saliva and sebum production (5/23)

MISCELLANEOUS

Aastrom Biosciences Inc. (ASTM)

BRC

Bone Repair Cell, a mixture of stem and progenitor cells derived from a patient's own bone marrow

Osteonecrosis of the femoral head

Company will being a pivotal trial with 120 patients (5/8)

AEterna Zentaris Inc. (AEZS) and Spectrum Pharmaceuticals (SPPI)

Ozarelix

Fourth-generation luteinizing hormone-releasing hormone antagonist

Lower urinary tract symptoms secondary to benign prostatic hyperplasia

Phase II data showed it was well tolerated and demonstrated statistically significant and clinically meaningful efficacy (5/23)

AlphaRx Inc. (OTC BB:ALRX) and Proprius Pharmaceuticals Inc.*

Indaflex

2.5% topical indomethacin cream

Osteoarthritis of the knee

Did not meet primary endpoints in a Phase II trial (5/15)

Altus Pharmaceuticals Inc. (ALTU)

ALTU-135

A blend of lipase, protease and amylase created with Altus' protein crystallization technology

For pancreatic enzyme replacement

Started a pair of pivotal efficacy and safety trials (5/10)

Basilea Pharmaceutica Ltd. (Switzerland; SWX:BSLN)

Alitretinoin

Once-daily oral treatment

Chronic hand eczema

Phase III data confirm the product's efficacy (5/21)

CollaGenex Pharmaceuticals Inc. (CGPI)

Incyclinide

Anti-inflammatory

Acne

Suspended further enrollment in the Phase II's 40 mg cohort after one patient experienced significant photo-toxicity (5/2); discontinued treatment of all enrolled patients in that cohort (5/7)

Cypress Bioscience Inc. (CYPB)

Milnacipran

Norepinephrine serotonin reuptake inhibitors

Fibromyalgia

A second Phase III trial achieved statistical significance at both doses and against both primary endpoints (5/23)

Cytos Biotechnology AG (Switzerland; SWX:CYTN)

CYT003-QbG10

Virus-like particle packaged with an immunostimulatory sequence

Allergic diseases

Phase II data showed two formulations were safe and well tolerated and demonstrated a statistically significant increase in the median allergen tolerance against baseline (5/15)

Emisphere Technologies Inc. (EMIS)

SMC021

Oral calcitonin

Osteoarthritis

Started a Phase III program (5/24)

Genaera Corp. (GENRD)

MSI-1436

Inhibits protein tyrosine phosphatase 1B, or PTP-1B; trodusquemine

Obesity

Dosing began in a Phase I trial (5/16)

Genzyme Corp. (GENZ)

Genz-112638

Oral therapy; a ceramide analogue designed to inhibit the enzyme glucosylceramide synthase

Gaucher's disease

Genzyme completed enrollment of its ongoing Phase II trial (5/16)

Gilead Sciences Inc. (GILD)

Aztreonam lysine

Inhaled antibiotic

Cystic fibrosis

Phase III data showed it met its primary efficacy endpoint of improved respiratory symptoms at day 28 (5/30)

Indevus Pharmaceuticals Inc. (IDEV)

Supprelin-LA

Histrelin acetate subcutaneous implant 50 mg

Central precocious puberty

FDA approved the product (5/3)

Inspire Pharmaceuticals Inc. (ISPH)

Epinastine nasal spray formulation

Seasonal allergic rhinitis

Phase II data demonstrated dose-related effects on the primary endpoint of improvement in total nasal symptom score, with the higher dose of 0.1% achieving statistical superiority over placebo (5/8)

Isotechnika Inc. (Canada; TSX:ISA)

ISA247

Immunosuppressive agent

Kidney transplant

Phase IIb data has shown improvement across all ISA247 dosing groups similar to that observed in the tacrolimus group; the product also showed reduced side effects vs. tacrolimus (5/7)

ISTA Pharmaceuticals Inc. (ISTA)

Bepotastine

A non-sedating, highly selective antagonist of the histamine 1 receptor that stabilizes mast cells and suppresses the migration of eosinophils into inflamed tissues

Allergic conjunctivitis

Phase II/III data showed both tested concentrations were statisitcally significant in the reduction of the first primary end-point, ocular itching, when dosed twice a day, and in one concentration when dosed once a day (5/8)

Kamada Ltd. (Israel; TASE:KMDA)

Alpha-1 antitrypsin

Aerosolized version using an optimized eFlow Electronic Nebulizer (PARI Pharma GmbH)

Congenital emphysema and cystic fibrosis

Concluded the first of two stages of its Phase I study (5/29)

Kamada Ltd. (Israel; TASE:KMDA) and PARI Pharma GmbH (Germany)

Alpha-1 antitrypsin

Aerosolized AAT delivered with an optimized eFlow device

AAT deficiency

Phase I data were positive (5/31)

LifeCycle Pharma A/S (Denmark; CSE:LCP)

LCP-Tacro

A once-daily tacrolimus tablet

Organ transplantation

Phase I data showed it delivers consistently higher bioavailability of about 50% compared to Prograf (5/31)

Limerick NeuroSciences Inc.*

LNS 5310

Candidate designed to improve bioavailability of existing drugs to reduce their neurotoxicity

To reduce nausea and vomiting

Started a Phase I trial (5/22)

Manhattan Pharmaceuticals Inc. (AMEX:MHA)

Oleoyl-estrone

Oral therapy; synthetic formulation

Obesity

Finished patient dosing in two Phase IIa trials, one for common obesity and the second for morbid obesity (5/10)

Marinus Pharmaceuticals Inc.*

Ganaxalone

3b-methylated synthetic analog of the neurosteroid allopregnanolone, a metabolite of progesterone

Partial onset seizures

Company is enrolling patients in a Phase IIb study (5/4)

MedImmune Inc. (MEDI)

IL-9

Targets interleukin-9

Asthma

Phase I data showed it was well tolerated (5/24)

MGI Pharma (MOGN)

Aquavan

Fospropofol disodium injection

For patients undergoing colonoscopy

Aquavan met its primary end-point in a pivotal Phase III trial (5/23)

Microbia Inc.*

Linaclotide

Peptide designed to act on guanylate cyclase C, a receptor found on intestinal cells

Irritable bowel syndrome

Phase II data showed it accelerated colonic transit and improved bowel function (5/21)

Millennium Pharmaceuticals Inc. (MLNM)

MLN0002

A monoclonal antibody designed to bind to the T-cell integrin alpha 4 beta 7

Gastrointestinal diseases

Resumed clinical development and initiated patient dosing in a Phase II program with healthy volunteers and ulcerative colitis patients (5/17)

Napo Pharmaceuticals Inc. (LSE:NAPL) and Trine Pharmaceuticals Inc.*

Crofelemer syndrome

Agent extracted from the rainforest plant Croton lechleri

Diarrhea-predominant irritable bowel

Phase IIa data showed it was safe and led to significant improvement in pain (5/23)

Nymox Pharmaceutical Corp. (NYMX)

NX-1207

Investigational agent for BPH

Benign prostatic hyperplasia

Phase I/II data showed NX-1207 had a mean improvement of 8.6 points in the primary outcome endpoint of AUA Symptom Score value 42 months after treatment vs. the 3.5 to 5 points reported in published studies of currently approved BPH drugs (5/7)

Obecure Ltd.* (Israel)

OBE101

Candidate comprised of betahistamine

Weight management

Launched a Phase II trial testing OBE101 in improving plasma lipid profiles of patients treated with Simvastatin, a generic cholesterol-lowering drug (5/16)

Palatin Technologies Inc. (AMEX:PTN)

Bremelanotide

First in a new class called melanocortin receptor agonists

Erectile dysfunction

Phase IIb data showed it improved both self-esteem and sexual relationship in men (5/23)

PDL BioPharma Inc. (PDLI)

Nuvion

Visilizumab; humanized monoclonal antibody

Intravenous steroid-refractory ulcerative colitis

Long-term follow up data from Phase I and Phase I/II trials demonstrated that treatment on day 1 and day 2 was adequately tolerated and resulted in a sustained clinical response for up to 310 days (5/22)

PTC Therapeutics Inc.*

PTC124

Oral agent that targets nonsense mutations

Duchenne muscular dystrophy

Interim Phase II data showed treatment was associated with increases in muscle dystrophin expression and reductions in serum creatinine kinase values in at least 50% of evaluable patients (5/4)

Regeneron Pharmaceuticals Inc. (REGN)

VEGF Trap-Eye

A fully human, soluble VEGF fusion protein

Neovascular form of age-related macular degeneration and diabetic macular edema

Phase II data were positive (5/9)

Repligen Corp. (RGEN)

RG1068

Synthetic human secretin; used with magnetic resonance imaging

To improve assessment of pancreatic duct structures

Phase II data showed an improvement in sensitivity of detection of structural abnormalities of the pancreatic duct of about 20%, with no loss in specificity (5/10)

Sirion Therapeutics Inc.*

ST-601

Topical ophthalmic emulsion containing the steroid compound difluprednate

Anterior uveitis

Started a Phase III program (5/1)

Sirion Therapeutics Inc.*

ST-603

Cyclosporine

Dry eye syndrome

Started a Phase III program (5/1)

Spectrum Pharmaceuticals Inc. (SPPI)

Ozarelix

Fourth-generation luteinizing hormone-releasing hormone

Benign prostatic hypertrophy

Reached its enrollment target in a Phase IIb trial

Sucampo Pharmaceuticals Inc.*

Amitiza

Lubiprostone, given 8 mcg twice a day

Irritable bowel syndrome

Study showed the active ingredient may improve symptom relief rates in adults in two Phase III trials (5/21)

Telomerase Activation Sciences Inc.*

TA-65

A telomerase activator

Anti-aging

Interim data from a 24-week study that included 36 male subjects ages 60 to 85 showed measurable anti-aging benefits in the areas of immune system function, vision, sexual function, skin condition and energy levels (5/15)

Theravance Inc. (THRX)

TD-5108

Gastrointestinal motility compound

Chronic constipation

Phase I data showed it has a pharmacokinetic profile consistent with once-daily dosing and prokinetic activity in healthy subjects (5/25)

Topigen Pharmaceuticals Inc.*

TPI ASM8

Inhaled RNA-targeted drug

Asthma

Phase II data showed significant inhibitory effects on allergen-induced responses (5/22)

Y's Therapeutics Inc.*

YSPSL

A recombinant molecule resulting from the fusion of P-selectin glycoprotein injury in liver transplant patients ligand and human IgG1

To prevent ischemic reperfusion

Started a Phase II trial (5/2)


Notes:

* Privately held.

BLA = Biologics license application; FDA = Food and Drug Administration; IND = Investigational new drug application; NDA = New drug application; SPA = Special protocol assessment.