Company* (Country; Symbol)

Product

Description

Indication

Status (Date)


AUTOIMMUNE

Amgen Inc. (AMGN)

Enbrel

Etanercept; tumor necrosis factor inhibitor

Psoriasis

Phase III data showed that 49% of patients treated with 50 mg twice weekly achieved at least a 75% improvement, compared to placebo, after three months (3/21)

Angiotech Pharmaceuticals Inc. (Canada; ANPI)

Paxceed

A Cremophor EL-free paclitaxel formulation

Psoriasis

Phase I data showed all nine patients had a positive response (3/19)

Centocor Inc. (unit of Johnson & Johnson)

Remicade (FDA-approved)

Infliximab; monoclonal antibody that specifically targets and irreversibly binds to TNF-alpha

Psoriasis

Phase II data showed 88% and 72% of patients treated with 5 mg/kg and 3 mg/kg of Remicade, respectively, experienced a greater than or equal to 75% improvement from baseline in Psoriasis Area Severity Index score, compared to 6% of placebo patients (3/21)

Genentech Inc. (NYSE:DNA) and XOMA Ltd. (XOMA)

Raptiva

Efalizumab; recombinant humanized monoclonal antibody

Psoriasis

Phase III data showed that after 12 weeks of Raptiva therapy, 27% of patients demonstrated 75% or greater Psoriasis Area Severity Index score improvement, compared to 4% of placebo patients (3/21)

Isotechnika Inc. (Canada; TSE:ISA)

ISA247

Immunosuppressive candidate

Psoriasis

Phase II data showed that ISA247 met or exceeded all primary and secondary efficacy and safety endpoints in patients with moderate to severe psoriasis (3/10)

La Jolla Pharmaceutical Co. (LJPC)

Riquent

B-cell toleragen; arrests the production of antibodies to dsDNA without suppressing healthy functions of the immune system

Lupus renal disease

Phase III data showed that Riquent lowers levels of antibodies to dsDNA in a statistically significant manner, although the trial did not reach statistical significance for its primary endpoint, time to renal flare (3/31)

CANCER

Aphton Corp. (APHT)

G17DT

Vaccine-like product that blocks the hormone gastrin 17

Pancreatic cancer

Phase III data showed a statistically significant overall median survival benefit of 83% for G17DT (3/4)

AVI BioPharma Inc. (AVII)

Neugene

Antisense drug targeting the oncogene c-myc

Cancer

Company completed Phase I trials (3/26)

Celgene Corp. (CELG)

Thalomid

Thalidomide; modulates levels of tumor necrosis factor alpha

Multiple myeloma

Data from the first pilot trials revealed a reduction in complex regional pain syndrome symptoms in three patients who continued with therapy for three months (3/21)

Cell Pathways Inc. (CLPA)

Aptosyn

Exisulind; small-molecule compound that augments apoptosis in precancerous cells

Non-small-cell lung cancer

Company completed enrollment in a Phase III trial of Aptosyn in combination with Taxotere (3/6)

CuraGen Corp. (CRGN)

CG53135

A protein therapeutic

Oral mucositis following chemotherapy

Company will begin a Phase I trial (3/4)

FeRx Inc.*

MTC-DOX

Magnetic Targeted Carrier drug delivery platform

Hepatocellular carcinoma

Phase I/II data showed that tumor localization of MTC-DOX was achieved in 31 of 33 patients and measurements of doxorubicin in plasma were undetectable or low (3/31)

Isis Pharmaceuticals Inc. (ISIS)

Affinitak

Inhibitor of protein kinase C-alpha expression

Non-small-cell lung cancer

Phase III data showed the drug failed to meet its primary end-point (3/17)

Oncolytics Biotech Inc. (Canada; TSE:ONC)

Reolysin

A human, reovirus-based product

Prostate cancer

Clinical results showed evidence of viral activity in five of six patients, and there were no safety concerns (3/31)

Oxford BioMedica plc* (UK)

TroVax

Cancer gene therapy product

Colorectal cancer

Company will begin a Phase II trial in up to 15 patients receiving chemotherapy for the first time to treat metastatic or inoperable cancer (3/3)

SuperGen Inc. (SUPG)

Decitabine

Inhibits DNA methyl-transferase activity

Advanced myelodysplastic syndrome

Company completed patient enrollment in a Phase III trial (3/17)

SuperGen Inc. (SUPG)

Decitabine

Inhibits DNA methyl-transferase activity

Leukemia

Phase I data showed that 21 of 23 patients achieved disease remission, with six of them alive and disease free as of May 2002 at a median of 3.3 years after stem cell transplantation; the median survival for the whole group was 17.2 months and disease-free survival was 8.9 months (3/31)

Telik Inc. (TELK)

TLK286

A small-molecule antitumor drug that is activated by GST-P1-1

Ovarian cancer

Company began a Phase III trial (3/27)

Tularik Inc. (TLRK)

T67

A drug that binds irreversibly to beta-tubulin

Hepatocellular carcinoma

Company enrolled the first patient in the registration trial of T67 (3/25)

Vion Pharmaceuticals Inc. (VION)

Triapine

Inhibitor of ribonucleotide reductase

Advanced leukemia

Company initiated a Phase I trial of Triapine in combination with cytarabine (3/31)

YM BioSciences Inc. (Canada; AIM:YMB; TSE:YM_PB)

Tesmilifene

Designed to enhance the chemotherapeutic effects of anthracyclines and taxanes

Advanced metastatic or recurrent breast cancer

Company will begin a Phase III trial (3/4)

CARDIOVASCULAR

Alteon Inc. (AMEX:ALT)

ALT-711

A.G.E. crosslink breaker

Diastolic heart failure

Phase IIa data showed a reduction in left ventricular mass (3/31)

AtheroGenics Inc. (AGIX)

AGI-1067

Oral anti-inflammatory drug candidate

Coronary artery disease

Company is beginning a Phase III trial in 160 U.S., Canadian and South African cardiac centers to evaluate AGI-1067's impact (3/13)

Cardiome Pharma Corp. (Canada; OTC BB:COMRF)

Oxypurinol

Belongs to a class of drugs that increases the pumping action of the heart without a proportionate increase in oxygen consumption by the organ

Congestive heart failure

Company began patient dosing in a Phase II/III study (3/11)

D-Pharm Ltd.* (Israel)

DP-b99

A neuroprotective agent that was shown to reduce brain infarct volumes and to help in recovery of neurological function

Acute stroke

Phase II data indicates that DP-b99 might be safely administered and that improvements were observed in clinical neurological scale scores (3/11)

Dyax Corp. (DYAX)

DX-88

Kallikrein inhibitor

Hereditary angioedema

Phase II data showed that specific inhibition of plasma kallikrein activity by DX-88 might be effective in treating acute symptoms in patients with hereditary angioedema (3/10)

Hemosol Inc. (Canada; HMSL; TSE:HML)

Hemolink

Hemoglobin raffimer; oxygen therapeutic designed to improve oxygen delivery via the circulatory system

Cardiac bypass grafting surgery

Hemosol is suspending enrollment in a Phase II trial based on a recommendation by its data safety monitoring board (3/13)

Medicure Inc. (Canada; TSE:MPH)

MC-1

Cardiovascular drug

Percutaneous coronary intervention

Phase II data showed MC-1 was safe and effective as a cardioprotective treatment to reduce damage to the heart associated with acute ischemic and reperfusion injury (3/31)

Northfield Laboratories Inc. (NFLD)

PolyHeme

Oxygen-carrying blood substitute that is derived from human blood but has a longer shelf life

For use in urgent blood loss

Northfield plans to proceed with a Phase III trial (3/6)

Nuvelo Inc. (NUVO; formerly Hyseq Pharmaceuticals Inc.)

Alfimeprase

A modified fibrolase that directly degrades fibrin when delivered through a catheter at the site of a blood clot

Peripheral arterial occlusion

Phase I data showed the product was safe and well tolerated with no related adverse events (3/27)

Texas Biotechnology Corp. (TXBI) and GlaxoSmithKline plc (UK)

Argatroban (FDA-approved)

A direct thrombin inhibitor anticoagulant

Acute ischemic stroke

Phase II data supported the tolerability of Argatroban, showing no statistically significant differences between Argatroban and placebo in symptomatic or asymptomatic intracranial hemorrhage (3/5)

Viron Therapeutics Inc.*(Canada)

VT-111

Anti-inflammatory protein

Acute coronary syndrome

Company completed a Phase I trial (3/6)

CENTRAL NERVOUS SYSTEM

Cypress Bioscience Inc. (CYPB)

Milnacipran

The first of a new class of agents known as NSRIs, or norepinephrine serotonin reuptake inhibitors

Fibromyalgia syndrome

Milnacipran was shown to statistically improve a number of primary and secondary hallmark symptoms of fibromyalgia, including occurence/intensity of pain and overall well being (3/21)

Endo Pharmaceuticals Inc. (ENDP)

EN3202

Extended-release oral form of the opioid oxymorphone

Severe, chronic low back pain

Clinical results showed that patients experienced significantly lower pain intensity scores when compared to placebo (3/20)

Forest Laboratories Inc. (NYSE:FRX)

Memantine

A moderate-affinity, uncompetitive N-methyl D-aspartate receptor antagonist that modulates glutamate levels

Alzheimer's disease

Clinical results showed no pharmacokinetic interactions between memantine and donepezil (Aricept) (3/10)

Repligen Corp. (RGEN)

RG1068

Synthetic human secretin

Autism

Company is beginning an open-label extension of its ongoing Phase III trials (3/25)

DIABETES

Amylin Pharmaceuticals Inc. (AMLN) and Eli Lilly and Co.

Exenatide LAR (formerly AC2993)

Sustained-release, subcutaneous injection of exenatide

Type II diabetes

Phase II data verified that sustained levels of exenatide are possible, supporting the continuation of a clinical program (3/19)

Aradigm Corp. (ARDM)

AERx iDMS

Insulin Diabetes Management System

Diabetes

Phase II data showed it was safe, well tolerated and produced reproducible dosing in smokers and patients with asthma (3/17)

Biovitrum AB* (Sweden)

BVT.3498

Highly selective inhibitor of the enzyme 11betaHSD1, yielding reduced tissue levels of cortisol

Type II diabetes

Company began a Phase II trial (3/25)

Flamel Technologies SA (France; FLML)

Basulin

Long-acting, subcutaneously administered formulation of human insulin based on Flamel's Medusa technology

Diabetes

Company reported positive results from a second trial showing Basulin provided at least the same efficacy and a similar pharma cokinetic profile as another long-acting insulin product, Lantus (3/27)

Ortec International Inc. (OTC BB:ORTC)

OrCel (FDA-approved)

Bilayered cellular matrix; collagen sponge seeded with allogeneic epidermal and dermal cells

Diabetic neuropathic foot ulcers

Clinical data showed that ulcers treated with OrCel had a faster rate of wound healing than those treated with the standard of care alone (3/17)

INFECTION

Acambis plc (UK; LSE:ACM)

ACAM2000

Vaccine

Smallpox

Phase I data showed that 99% of patients achieved the accepted indication of protective immunogenicity - the development of a pockmark on the skin (3/11)

Anadys Pharmaceuticals Inc.*

ANA245

Antiviral that elevates levels of interferon-alpha and provides antiviral and antimetastatic activity in a variety of murine systems

Hepatitis C

Company completed a Phase Ia study (3/3)

Bavarian Nordic A/S (Denmark; CSE:BAVA)

MVA-BN nef

Vaccine

HIV

Phase I/II results showed that up to 11 months after stopping anti-retroviral therapy, the levels of HIV in seven patients remained below their pre-therapy level (3/5)

BioMarin Pharmaceutical Inc. (BMRN)

Aryplase

Recombinant human arylsulfatase B; enzyme replacement therapy

Mucopolysac- charidosis VI

Phase II data indicated that Aryplase was well tolerated and associated with improvements in several clinical endpoints (3/14)

CollaGenex Pharmaceuticals Inc. (CGPI)

Metastat

Orally active angiogenesis inhibitor

HIV-related Kaposi's sarcoma

Company completed enrollment in a Phase II study (3/28)

Cytovax Biotechnologies Inc. (Canada; TSE:CXB)

Cytovaxine

A peptide vaccine that uses the company's AntiAdhesin Technology to prevent infection

To prevent infection caused by Pseudomonas aeruginosa

Company completed a Phase I trial of Cytovaxine (3/28)

Pharmasset Inc.*

Racivir

Nucleoside antiviral agent

HIV

Phase Ib/IIa data showed favorable results (3/26)

Versicor Inc. (VERS)

Anidulafungin

Intravenous infusion

Esophageal candidiasis

Phase III data showed the drug hit its primary endpoint, demonstrating the antifungal agent's non-inferiority to fluconazole; it did not meet a secondary end-point when its relapse rate was at 35.6% compared to 10.5% for fluconazole (3/18)

MISCELLANEOUS

Alkermes Inc. (ALKS)

Vivitrex

A formulation of naltrexone based on Alkermes' Medisorb injectable

Alcohol dependence

Company completed enrollment of more than 600 patients in its pivotal Phase III trial (3/31)

Arriva Pharmaceuticals Inc.* and Baxter Healthcare Corp.

--

Alpha 1-antitrypsin therapy

Hereditary emphysema

Companies began a Phase I trial (3/4)

BioSante Pharmaceuticals Inc. (OTC BB:BISP)

Bio-E-Gel

Estradiol topical gel

Menopausal symptoms (hot flashes)

Company completed its Phase II/III trial of Bio-E-Gel (3/3)

Dynavax Technologies Corp.*

AIC

Anti-allergy immunotherapy

Ragweed allergy

Phase II data showed AIC appears to provide protection against ragweed allergy (3/11)

Dynavax Technologies Corp.*

ISS

Immuno-stimulatory DNA sequence

Asthma

Phase I data demonstrated the safety and biological activity of its inhaled ISS to treat asthma (3/7)

Genzyme General (GENZ)

Myozyme

Recombinant human acid alpha-glucosidase enzyme

Pompe disease

Company began enrollment in a U.S. and European trial (3/19)

Inspire Pharmaceuticals Inc. (ISPH)

INS37217 Intranasal

A non-preserved nasal spray formulation

Perennial allergic rhinitis

Company completed enrollment in a 630-patient trial (3/6)

MediWound Ltd.* (Israel)

Debrase Gel Dressing

Engineered from pineapple stems

Thermal burns

Company began Phase IIb trials in the U.S. and Europe (3/5**)

NicOx SA (France; Nouveau Marche:NICOX)

AZD3582

First of a new class of analgesic and anti-inflammatory drugs known as COX-inhibiting nitric oxide donators

Gastrointestinal ulcers

Phase II data showed AZD3582 failed to meet its primary end-point, but the company said that due to a lower than predicted rate of gastrointestinal ulcers in the group treated, the study was underpowered; the compound met secondary endpoints (3/11)

Regeneron Pharmaceutical Inc. (REGN)

Axokine

Genetically reengineered version of a naturally occurring human protein known as ciliary neurotrophic factor

Obesity

Axokine met primary and secondary endpoints in a Phase III trial, but the incidence of neutralizing antibodies was 70% (3/31)

Tanox Inc.
(TNOX)

TNX-901

A humanized anti-IgE antibody

Peanut allergy

Phase II data were positive (3/11)

Vivus Inc.
(VVUS)

Alista

Formulation of alprostadil applied locally to the female genitalia

Female sexual arousal disorder

Company began recruitment for a Phase II trial (3/17); clinical results showed a statistically significant improvement in the primary endpoint of satisfactory sexual arousal and/or orgasm in the 400-mg dose group; results in the 200-mg and 800-mg dose groups demonstrated positive trends for the primary end-point but did not reach statistical significance (3/31)


Notes:

* Privately held company

** Denotes the date the item ran in BioWorld International.

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