Combining Cas9 RNP with ssODN mediates efficient HSPC genome editing of sickle mutation Nov. 14, 2016
New variant in SERPINC1 may be a disease-causing mutation for antithrombin-III type I deficiency Oct. 26, 2016
EMA issues positive opinion recommending orphan drug designation for La Jolla's LJPC-401 Oct. 25, 2016
Phase II results on OMS-721 in stem cell transplant-associated thrombotic microangiopathy Oct. 24, 2016
FIT phase III trials and open-label extension study show consistent benefit of fostamatinib Oct. 21, 2016