FDA grants fast track designation for CLBS-03 for the treatment of recent onset type 1 diabetes July 29, 2016
European orphan drug designation awarded to volanesorsen for familial partial lipodystrophy July 29, 2016
Methanobactin reverses mitochondrial impairment and acute liver failure in model of Wilson disease July 29, 2016
New phase I trial explores use of lentivirus alpha-gal A transduced CD34+ cells in Fabry disease July 29, 2016