Preliminary clinical data on CRISPR/Cas9 gene-editing therapy CTX-001 in severe hemoglobinopathies Nov. 20, 2019
FDA approves Adakveo to reduce vaso-occlusive crises in patients with sickle cell disease Nov. 18, 2019
FDA approves Reblozyl for anemia in beta thalassemia requiring regular RBC transfusions Nov. 11, 2019