Benitec’s BB-301 cleared to enter clinic in US for oculopharyngeal muscular dystrophy-related dysphagia

June 27, 2023

Benitec Biopharma Inc. has received FDA clearance of its IND application for BB-301, its silence and replace gene therapy for the treatment of oculopharyngeal muscular dystrophy (OPMD)-related dysphagia.

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Illustration of a glowing circle to represent circRNA

ASGCT 2026: Circular RNA, the new beast in gene and cell therapy

BioWorld

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Alzheimer’s, beyond the brain

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Advancing the 'best of both' – BMS, Hengrui enter $15.2B deal

BioWorld

In a deal potentially worth up to $15.2 billion, Jiangsu Hengrui Pharmaceuticals Co. Ltd. is joining efforts with Bristol Myers Squibb Co. to advance 13 early...