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BioWorld Science

July 12, 2016

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FDA grants orphan drug designation to gene therapy for the treatment of retinitis pigmentosa

MorphoSys initiates phase II/III trial of MOR-208 with bendamustine in DLBCL

FDA confers orphan drug status to angiogenesis inhibitor nintedanib

FDA approves first compassionate use of masitinib for ALS

Alexion Pharmaceuticals' ALXN-1540 receives U.S. orphan drug designation for Crigler-Najjar syndrome

Mazindol granted orphan drug designation in U.S.

Gilead Sciences and Institute of Organic Chemistry and Biochemistry patent anti-HIV agents

Pontificia Universidad Catolica de Chile patent reveals antineoplastic compounds

Celldex Therapeutics initiates phase I/II study of CDX-014 in renal cell carcinoma

MIT and The Broad Institute report dopamine D2 receptor ligands

MAPK inhibitors described in Axikin Pharmaceuticals patent

Kyoto University and Nagasaki University disclose gamma delta T cell inducers

Coherus BioSciences' study of pegfilgrastim biosimilar meets coprimary endpoints

AZD-5363 after radiotherapy improves head and neck cancer tumor control in vivo but not in vitro

AdAlta to raise funds to support clinical studies of candidate for IPF

European Investment Bank loan supports R&D activities at Valneva

NIH grant supports Cellex's development of rapid test for detection of CPOs

Novel multiple sclerosis susceptibility loci identified in GWAS

Cell Medica announces acquisition of Delenex Therapeutics

FDA approves monthly single-dose evolocumab system

rTSST-1v vaccine shows potential for the prevention of TSST-1-dependent disease

Leukemia & Lymphoma Society makes second investment in Kiadis to support development of ATIR-101

FDA approves Xiidra to treat signs and symptoms of dry eye disease

Sucampo Pharmaceuticals decides to discontinue development of cobiprostone

Cantabio and Purdue Research Foundation to collaborate on DJ-1-targeting drugs

AbbVie's ABT-414 wins rare pediatric disease designation from FDA

AOP Orphan Pharmaceuticals' Rapibloc approved in Europe

WARS2 gene linked to angiogenesis within and outside the heart

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