All Clarivate Analytics websites use cookies to improve your online experience. They were placed on your computer when you launched this website. You can change your cookie settings through your browser.
Alexion Pharmaceuticals Inc., of New Haven, Conn., reported new interim data from a trial testing Kanuma (sebelipase alfa) in patients with rapidly progressive lysosomal acid lipase deficiency at the NASPGHAN Annual Meeting in Las Vegas. Of the 10 infants treated with Kanuma, nine survived beyond 1 year of age, compared to a median age of death of 3.7 months with mortality by 1 year of nearly 100 percent for historically untreated infants.