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BioWorld - Friday, May 15, 2026
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Home » Actelion redux? Fabry bid enters phase III as Idorsia working with full pipeline
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Actelion redux? Fabry bid enters phase III as Idorsia working with full pipeline

May 17, 2018
By Randy Osborne
With the countdown continuing to the Aug. 13 PDUFA date for Amicus Therapeutics Inc.'s migalastat in Fabry disease, Idorsia Ltd. has enrolled its first patient in a phase III registration study investigating the oral monotherapy lucerastat in that indication as well.
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