Akari announces trial design for pivotal phase III study of nomacopan in pediatric HSCT-TMA Dec. 3, 2019
Preliminary clinical data on CRISPR/Cas9 gene-editing therapy CTX-001 in severe hemoglobinopathies Nov. 20, 2019
FDA approves Adakveo to reduce vaso-occlusive crises in patients with sickle cell disease Nov. 18, 2019