FDA accepts IND application for phase I/II study of AVR-RD-04 gene therapy for cystinosis Jan. 21, 2019
Top-line data presented from phase II study of NYX-2925 in painful diabetic peripheral neuropathy Jan. 17, 2019
Targeting transferrin receptor protein 2 knockout alleviates anemia in a model of beta-thalassemia Jan. 15, 2019
Alnylam explores ALN-AAT02 in phase I/II study for ZZ type AAT deficiency liver disease Jan. 14, 2019
Regulator of calcineurin 1 suppresses nonshivering thermogenesis by two different mechanisms Jan. 11, 2019