Phase I/II results with pegzilarginase in arginase deficiency support upcoming pivotal trial Sep. 6, 2018
Proof-of-concept data presented from PHYOX phase I study of DCR-PHXC in primary hyperoxaluria Sep. 6, 2018
Phase I/IIa study of SYNB-1618 in healthy volunteers establishes dose for patients with PKU Sep. 4, 2018