Dual sHE inhibitor/PPAR-gamma agonist shows benefits to treat metabolic syndrome and diabetes in rat Sep. 12, 2018
Phase I/II results with pegzilarginase in arginase deficiency support upcoming pivotal trial Sep. 6, 2018
Proof-of-concept data presented from PHYOX phase I study of DCR-PHXC in primary hyperoxaluria Sep. 6, 2018