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BioWorld - Tuesday, March 3, 2026
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» Retrotope looks to FDA for guidance in ultra-rare pediatric dystrophy
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Retrotope looks to FDA for guidance in ultra-rare pediatric dystrophy
Oct. 6, 2021
By
Lee Landenberger
Privately held Retrotope Inc., the only company currently in the clinic studying the ultra-rare and fatal neurological disorder infantile neuroaxonal dystrophy, has new data it hopes to present to the FDA early next year.
BioWorld
Clinical
Neurology/psychiatric