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Home » Intellia touting possible ‘functional cure’ for HAE with gene-editing candidate
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Intellia touting possible ‘functional cure’ for HAE with gene-editing candidate

June 12, 2023
By Jennifer Boggs
Promising early data continue to roll out for Intellia Therapeutics Inc.’s hereditary angioedema (HAE) candidate, NTLA-2002, with one of the earliest treated patients in the phase I study remaining attack-free for more than a year. But it was the systemic CRISPR candidate’s potential as a one-time treatment that generated the most discussion on the company’s call as investors tried to assess its potential advantage in a crowded HAE market.
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