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BioWorld - Monday, May 11, 2026
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Home » RNA gene writing technology to reverse phenylketonuria and sickle cell disease
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Drug Design, Drug Delivery & Technologies

RNA gene writing technology to reverse phenylketonuria and sickle cell disease

June 21, 2023
By Mar de Miguel
With CRISPR-Cas9 technology making its way toward clinical practice, laboratories are studying different gene-editing techniques, from base editors to prime editors, to correct mutations associated with various pathologies. Researchers at Tessera Therapeutics Inc. have been inspired by retrotransposons to develop a tool for editing DNA using RNA and reverse diseases such as phenylketonuria (PKU) or sickle cell disease (SCD).
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