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BioWorld - Saturday, May 16, 2026
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Home » Historic MHRA exa-cel win bagged, Crispr/Vertex await FDA nod
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Historic MHRA exa-cel win bagged, Crispr/Vertex await FDA nod

Nov. 16, 2023
By Randy Osborne
With a landmark U.K. approval in hand for Casgevy (exagamglogene autotemcel [exa-cel]) to treat sickle cell disease and transfusion-dependent beta thalassemia, Crispr Therapeutics AG and partner Vertex Therapeutics Inc. are turning their attention to the PDUFA dates set by the U.S. FDA for the treatment in both conditions.
BioWorld Regulatory Hematologic Europe MHRA

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