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BioWorld - Friday, February 13, 2026
Breaking News: BioWorld Science 2025 Year in ReviewSee today's BioWorld Science
Home » Next-generation genome editing tools surpass CRISPR milestone
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Drug Design, Drug Delivery & Technologies

Next-generation genome editing tools surpass CRISPR milestone

Dec. 28, 2023
By Anette Breindl and Mar de Miguel
Modifying a patient’s DNA is no longer just for science fiction novels. The CRISPR gene editing technique developed by Jennifer Doudna and Emmanuelle Charpentier only took 10 years to reach the market as Casgevy (exagamglogene autotemcel/exa-cel, Vertex Pharmaceuticals Inc.), treating congenital pathologies such as β-thalassemia and severe sickle cell disease (SCD). But science does not stop.
BioWorld Science Bioengineering Drug design, drug delivery and technologies Gene therapy Genetic/congenital

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