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BioWorld - Thursday, March 12, 2026
Breaking News: Trump administration impacts continue to roil the life sciences sectorSee today's BioWorld Science
Home » New regulatory playbook to guide AAV gene therapy development for rare diseases
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Drug Design, Drug Delivery & Technologies

New regulatory playbook to guide AAV gene therapy development for rare diseases

Feb. 7, 2024
The Foundation for the National Institutes of Health (FNIH) has announced the online publication of the first playbook designed to help accelerate the development of adeno-associated virus (AAV) gene therapies for rare diseases.
BioWorld Science Regulatory Drug design, drug delivery and technologies Gene therapy U.S. FDA NIH

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