Opus Genetics’ OPGx-BEST1 cleared to enter clinic

Aug. 19, 2025

Opus Genetics Inc. has obtained IND clearance from the U.S. FDA application for OPGx-BEST1, a gene therapy for the treatment of bestrophin-1 (BEST1)-related inherited retinal disease (IRD).

BioWorld Science Regulatory Genetic/congenital Ocular Gene therapy FDA IND

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