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BioWorld - Saturday, April 4, 2026
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Home » Study identifies ASO targeting UBE3A-ATS for Angelman syndrome
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Neurology/psychiatric

Study identifies ASO targeting UBE3A-ATS for Angelman syndrome

Sep. 22, 2025
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Angelman syndrome (AS) is a rare neurodevelopmental disorder caused by the loss of function of the maternally inherited ubiquitin E3 ligase UBE3A gene. AS is characterized by severe symptoms, including lack of speech, epilepsy, developmental and motor skills delays, sleep disturbances and cognitive impairment. Currently, no treatments are available for this disease.
BioWorld Science Neurology/psychiatric

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