FDA clears IND for phase I/II study of VX-880 stem cell-derived therapy for type 1 diabetes Feb. 1, 2021
PRV-3279 prevents immunogenicity in a preclinical model of gene therapy for Pompe disease Jan. 29, 2021
Primary endpoint met in ACTIVATE-T trial of mitapivat in transfused patients with PK deficiency Jan. 27, 2021
One-year data from SPIRIT Extension study of relugolix combination therapy in endometriosis Jan. 26, 2021