Lentiviral gene therapy with OTL-101 shows safety and efficacy in patients with ADA-SCID Feb. 26, 2019
Novel double-hit pre-eclampsia mouse model mimics human clinical course of the condition Feb. 25, 2019
Euglycemic ketoacidosis in SGLT2 inhibitor-treated rats requires dehydration and insulinopenia Feb. 25, 2019
Ultragenyx presents positive 24-week data from first cohort of phase I/II study of DTX-401 Feb. 22, 2019