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BioWorld - Thursday, March 19, 2026
Home » Topics » Genetic/congenital, BioWorld Science

Genetic/congenital, BioWorld Science
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RNA strand
Endocrine/Metabolic

Wave Life Sciences reports data on WVE-006 in AATD mouse model

Sep. 29, 2022
Wave Life Sciences Ltd. has highlighted progress with WVE-006, its preclinical Aimer (A-to-I RNA base editing) oligonucleotide candidate for the treatment of alpha-1 antitrypsin deficiency (AATD).
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Mitochondria illustration
Genetic/congenital

Pretzel Therapeutics launches with focus on mitochondrial biology

Sep. 13, 2022
Pretzel Therapeutics Inc. has launched with a $72.5 million series A financing to pioneer novel therapies to modulate mitochondrial function to treat rare genetic diseases and common diseases of aging.
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