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BioWorld - Friday, February 6, 2026
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Home » Second opinion: US FDA panel follows eli-cell nod with confirmation of beti-cel benefit
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Second opinion: US FDA panel follows eli-cell nod with confirmation of beti-cel benefit

June 10, 2022
By Randy Osborne
After surprising Wall Street by unanimously voting in favor of the gene therapy elivaldogene autotemcel (eli-cel) for early active cerebral adrenoleukodystrophy from Bluebird Bio Inc., the FDA’s Cellular, Tissue and Gene Therapies Advisory Committee met again June 10, this time to examine the risk-benefit profile of the company’s betibeglogene autotemcel (beti-cel) for people with transfusion-dependent beta-thalassemia.
BioWorld Regulatory Hematologic Gene therapy U.S. FDA

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