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BioWorld - Tuesday, March 3, 2026
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Home » Biomarin has challengers for treating rare, genetic achondroplasia
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Biomarin has challengers for treating rare, genetic achondroplasia

Oct. 25, 2023
By Lee Landenberger
Four other companies want to replicate Biomarin Pharmaceuticals Inc.’s recent success as they seek approvals to treat the rare but most prevalent genetic form of dwarfism, achondroplasia. The U.S. FDA approved the sNDA for injectable Voxzogo (vosoritide), fibroblast growth factor receptor 3 (FGFR3) inhibitor from Biomarin on Oct. 20.
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