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BioWorld - Wednesday, February 4, 2026
Breaking News: BioWorld Science 2025 Year in ReviewSee today's BioWorld Science
Home » NBD1 stabilizers rescue F508del-CFTR function
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Genetic/congenital

NBD1 stabilizers rescue F508del-CFTR function

Nov. 5, 2025
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Researchers from Sionna Therapeutics Inc. presented preclinical efficacy data on first-in-class NBD1 stabilizers and their use in combination with complementary modulators to correct cystic fibrosis transmembrane conductance receptor (CFTR) assembly.
BioWorld Science Conferences Genetic/congenital

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