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BioWorld - Tuesday, January 13, 2026
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» Charity bringing to EU market gene therapy spurned by pharma
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Charity bringing to EU market gene therapy spurned by pharma
Nov. 14, 2025
By
Nuala Moran
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Fifteen years since the first patient was treated, and after being ditched by two companies, the EMA is recommending approval of Waskyra (etuvetidigene autotemcel), the first gene therapy for treating Wiskott-Aldrich syndrome.
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