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BioWorld - Friday, May 8, 2026
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Home » Sarepta shifts to efficacy outlook with three-year Elevidys DMD data
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Sarepta shifts to efficacy outlook with three-year Elevidys DMD data

Jan. 26, 2026
By Jennifer Boggs
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After a roller coaster of a year for Duchenne muscular dystrophy (DMD) gene therapy Elevidys (delandistrogene moxeparvovec), Sarepta Therapeutics Inc. looks to focus on the efficacy narrative in 2026, starting with newly unveiled three-year data showing durable efficacy across all key motor function assessments for treated DMD patients vs. external controls.
BioWorld Clinical Musculoskeletal Gene therapy U.S.

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