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BioWorld - Tuesday, January 20, 2026
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Home » Astellas stops dosing gene therapy for rare neuromuscular disease after trial's fourth SAE
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Astellas stops dosing gene therapy for rare neuromuscular disease after trial's fourth SAE

Sep. 1, 2021
By Michael Fitzhugh
Astellas Pharma Inc. has halted further dosing of the experimental X-linked myotubular myopathy (XLMTM) gene therapy AT-132 (resamirigene bilparvovec) after one participant in the ongoing Aspiro study experienced a serious adverse event (SAE) of abnormal liver function.
BioWorld Clinical Musculoskeletal Neurology/psychiatric Gene therapy

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