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BioWorld - Wednesday, April 15, 2026
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Home » FDA puts PTC's US Huntington’s disease study enrollment on hold
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FDA puts PTC's US Huntington’s disease study enrollment on hold

Oct. 19, 2022
By Lee Landenberger
The U.S. FDA wants more data on PTC-518 before PTC Therapeutics Inc.'s phase II study of Huntington’s disease can continue enrollment. While stopped in the U.S., the study of the oral, small-molecule splicing modifier still is enrolling participants at sites in several European countries and in Australia.
BioWorld Clinical Regulatory Neurology/psychiatric FDA

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