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BioWorld - Tuesday, December 9, 2025
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» NS Pharma’s NS-051 designated orphan drug for DMD
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Neurology/psychiatric
NS Pharma’s NS-051 designated orphan drug for DMD
Sep. 22, 2025
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NS Pharma Inc.’s NS-051 (NCNP-04) has been awarded orphan drug designation by the FDA for the treatment of Duchenne muscular dystrophy (DMD) in patients amenable to exon 51 skipping.
BioWorld Science
Regulatory
Neurology/psychiatric
FDA
Orphan drug