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BioWorld - Thursday, April 16, 2026
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Home » On new Huntington’s data, FDA lifts partial hold on PTC phase II
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On new Huntington’s data, FDA lifts partial hold on PTC phase II

June 20, 2024
By Lee Landenberger
A nearly two-year-old partial clinical hold has been lifted by the U.S. FDA on PTC Therapeutics Inc.’s pivotal phase II study in Huntington’s disease. The agency had paused enrollment in October 2022, saying it wanted more data on PTC-518, an orally bioavailable small-molecule splicing modifier, before enrollment could continue.
BioWorld Clinical Regulatory Neurology/psychiatric Small molecule FDA

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