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BioWorld - Tuesday, July 21, 2026
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Home » FDA ‘blacklist’ in DMD? Legislator slams PTC turndown
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FDA ‘blacklist’ in DMD? Legislator slams PTC turndown

March 11, 2026
By Randy Osborne
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The strife-marked Duchenne muscular dystrophy (DMD) space drew forth another outspoken political figure in the shape of Sen. Ron Johnson (R-Wisc.), who said he was “enraged” by the U.S. FDA’s refusal to consider PTC Therapeutics Inc.’s Translarna (ataluren) for the treatment of nonsense mutation disease.
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