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BioWorld - Friday, March 13, 2026
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Home » FDA ‘blacklist’ in DMD? Legislator slams PTC turndown
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FDA ‘blacklist’ in DMD? Legislator slams PTC turndown

March 13, 2026
By Randy Osborne
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The strife-marked Duchenne muscular dystrophy (DMD) space drew forth another outspoken political figure in the shape of Sen. Ron Johnson (R-Wisc.), who said he was “enraged” by the U.S. FDA’s refusal to consider PTC Therapeutics Inc.’s Translarna (ataluren) for the treatment of nonsense mutation disease.
BioWorld Regulatory Musculoskeletal Small molecule U.S. FDA

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